- Conditions
- Variant Late-Infantile Neuronal Ceroid Lipofuscinosis
- Interventions
- AT-GTX-501
- Genetic
- Lead sponsor
- Emily de los Reyes
- Other
- Eligibility
- 1 Year and older
- Enrollment
- 13 participants
- Healthy volunteers
- Healthy volunteers not accepted
- Timeline
- 2016 – 2024
- U.S. locations
- 1
- States / cities
- Columbus, Ohio
Source: ClinicalTrials.gov public record
Updated Oct 23, 2025 · Synced May 21, 2026, 9:39 PM EDT