Study to Evaluate Blood Cell Lines From Patients With Gaucher Disease
Public ClinicalTrials.gov record NCT00351156. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Official title
A Multicenter Study to Evaluate and Characterize the Ex Vivo Effect of Pharmacological Chaperone Therapy in Blood Cell Lines Derived From Patients With Gaucher Disease
Study identification
- NCT ID
- NCT00351156
- Recruitment status
- Completed
- Study type
- Observational
- Phase
- Not listed
- Lead sponsor
- Amicus Therapeutics
- Industry
- Enrollment
- 50 participants
Conditions and interventions
Conditions
Interventions
- Blood sample Procedure
Procedure
Eligibility (public fields only)
- Age range
- Not listed
- Sex
- All
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Jun 30, 2006
- Primary completion
- Feb 28, 2007
- Completion
- Feb 28, 2007
- Last update posted
- Aug 18, 2010
2006 – 2007
United States locations
- U.S. sites
- 7
- U.S. states
- 7
- U.S. cities
- 7
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| University of California - San Francisco | San Francisco | California | 94143 | — |
| University Research Foundation for Lysosomal Storage Diseases, Inc. | Coral Springs | Florida | 33065 | — |
| Emory University Lysosomal Storage Disease Center | Decatur | Georgia | 30033 | — |
| National Institute of Neurological Disorders and Stroke, NIH | Bethesda | Maryland | 20892 | — |
| New York University School of Medicine, Neurogenetics Department | New York | New York | 10016 | — |
| Lysosomal Disease Center, Cincinnati Children's Hospital | Cincinnati | Ohio | 45229 | — |
| Children's Hospital of Philadelphia | Philadelphia | Pennsylvania | 19104 | — |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT00351156, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted Aug 18, 2010 · Synced Apr 29, 2026
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Open the official record
The complete protocol, eligibility criteria, and contact information for NCT00351156 live on ClinicalTrials.gov.