ClinicalTrials.gov record
Completed Phase 2 Interventional Results available

HSCT for High Risk Inherited Inborn Errors

ClinicalTrials.gov ID: NCT00383448

Public ClinicalTrials.gov record NCT00383448. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 5, 2026, 2:53 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Treatment of High Risk, Inherited Lysosomal And Peroxisomal Disorders by Reduced Intensity Hematopoietic Stem Cell Transplantation

Study identification

NCT ID
NCT00383448
Recruitment status
Completed
Study type
Interventional
Phase
Phase 2
Lead sponsor
Masonic Cancer Center, University of Minnesota
Other
Enrollment
38 participants

Conditions and interventions

Interventions

  • Alemtuzumab Drug
  • Clofarabine Drug
  • Cyclosporine A Device
  • Hematopoietic Stem Cell Transplantation Biological
  • Hydroxyurea Drug
  • Melphalan Drug
  • Total body Irradiation Procedure
  • mycophenylate mofetil Drug

Drug · Device · Biological + 1 more

Eligibility (public fields only)

Age range
Up to 70 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Aug 31, 2006
Primary completion
Aug 31, 2014
Completion
Aug 31, 2014
Last update posted
Jul 10, 2019

2006 – 2014

United States locations

U.S. sites
1
U.S. states
1
U.S. cities
1
Facility City State ZIP Site status
Masonic Cancer Center, University of Minnesota Minneapolis Minnesota 55455

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT00383448, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Jul 10, 2019 · Synced May 5, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT00383448 live on ClinicalTrials.gov.

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