Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or III

ClinicalTrials.gov ID: NCT00439569

Public ClinicalTrials.gov record NCT00439569. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

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ClinicalTrials.gov public records Last synced May 16, 2026, 9:28 AM EDT

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Official title

Phase I/IIa Clinical Trial of Sodium Phenylbutyrate in Pediatric Subjects With Type II/III Spinal Muscular Atrophy

Study identification

NCT ID: NCT00439569
Recruitment status: Terminated
Study type: Interventional
Phase: Phase 1, Phase 2
Lead sponsor: Westat; Other
Enrollment: 9 participants

Conditions and interventions

Conditions

Interventions

sodium phenylbutyrate Drug

Drug

Eligibility (public fields only)

Age range: 2 Years to 11 Years
Sex: All
Healthy volunteers: Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date: Dec 31, 2007
Primary completion: Jul 31, 2008
Completion: Jul 31, 2008
Last update posted: Sep 7, 2010

2008

United States locations

U.S. sites: 5
U.S. states: 5
U.S. cities: 5

Facility	City	State	ZIP	Site status
Stanford University Medical Center, 300 Pasteur Drive, Room A343	Stanford	California	94305-5235	—
Washington University Medical School, Washington University, 660 S. Euclid Avenue, Box 8111	St Louis	Missouri	63110	—
Columbia University, 180 Fort Washington Avenue, 5th Floor	New York	New York	10032	—
The Children's Hospital of Philadelphia, Clinical Trials Office, A-230, 34th St. and Civic Center Boulevard	Philadelphia	Pennsylvania	19104-4399	—
University of Texas Southwestern Medical Center at Dallas, Division of Pediatric Neurology, Children's Medical Center of Dallas, Ambulatory Care Pavilion, 2350 Stemmons Freeway, Suite #5074	Dallas	Texas	75207	—

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows: Public field values for ClinicalTrials.gov record NCT00439569, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do: No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from: Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh: Last update posted Sep 7, 2010 · Synced May 16, 2026

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The complete protocol, eligibility criteria, and contact information for NCT00439569 live on ClinicalTrials.gov.

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