ClinicalTrials.gov record
Completed Phase 1Phase 2 Interventional Results available

A Phase I Dose Finding and Safety Study of Oral LDE225 in Children and a Phase II Portion to Assess Preliminary Efficacy in Recurrent or Refractory MB

ClinicalTrials.gov ID: NCT01125800

Public ClinicalTrials.gov record NCT01125800. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 17, 2026, 3:17 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase I/II Study of LDE225 in Pediatric Patients With Recurrent or Refractory Medulloblastoma or Other Tumors Potentially Dependent on the Hedgehog-signaling Pathway and Adult Patients With Recurrent or Refractory Medulloblastoma

Study identification

NCT ID
NCT01125800
Recruitment status
Completed
Study type
Interventional
Phase
Phase 1, Phase 2
Lead sponsor
Novartis Pharmaceuticals
Industry
Enrollment
76 participants

Conditions and interventions

Eligibility (public fields only)

Age range
12 Months to 18 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jan 31, 2011
Primary completion
Sep 30, 2014
Completion
Sep 30, 2014
Last update posted
Mar 19, 2017

2011 – 2014

United States locations

U.S. sites
4
U.S. states
4
U.S. cities
4
Facility City State ZIP Site status
Children's Healthcare of Atlanta Childern Hosp - ATL Atlanta Georgia 30342
Sidney Kimmel Comprehensive Cancer Center/Johns Hopkins Med. John Hopkins Baltimore Maryland 21231
Dana Farber Cancer Institute DFCI (3) Boston Massachusetts 02115
Seattle Children's Hospital CPKC412A2114 Seattle Washington 98105

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 10 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT01125800, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Mar 19, 2017 · Synced May 17, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT01125800 live on ClinicalTrials.gov.

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