Open-Label Single Ascending Dose of Adeno-associated Virus Serotype 8 Factor IX Gene Therapy in Adults With Hemophilia B
Public ClinicalTrials.gov record NCT01687608. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Official title
A Phase 1/2 Open-Label, Single Ascending Dose Trial of a Self-Complementing Optimized Adeno-associated Virus Serotype 8 Factor IX Gene Therapy (AskBio009) in Adults With Hemophilia B
Brief summary
Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.
The purpose of this study is to evaluate the safety of single ascending IV doses of a Factor IX (FIX) Gene Therapy in up to 16 Adults with Hemophilia B.
Study identification
- NCT ID
- NCT01687608
- Recruitment status
- Active, not recruiting
- Study type
- Interventional
- Phase
- Phase 1, Phase 2
- Enrollment
- 30 participants
Conditions and interventions
Conditions
Eligibility (public fields only)
- Age range
- 18 Years to 75 Years
- Sex
- Male
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Feb 11, 2013 (Actual)
- Primary completion
- Jan 17, 2030 (Estimated)
- Completion
- Jan 17, 2030 (Estimated)
- Last update posted
- Mar 20, 2026
2013 – 2030
United States locations
- U.S. sites
- 15
- U.S. states
- 12
- U.S. cities
- 14
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| Orthopaedic Hemophilia Treatment Center | Los Angeles | California | 90007 | — |
| Children's Hospital Los Angeles | Los Angeles | California | 90027 | — |
| University of California Davis Medical Center | Sacramento | California | 95817 | — |
| University of California at San Diego Medical Center | San Diego | California | 92103-8651 | — |
| U of Colorado School of Medicine, Hemophilia & Thrombosis Treatment Center | Aurora | Colorado | 80045 | — |
| Emory University | Atlanta | Georgia | 30322 | — |
| Rush University Medical Center | Chicago | Illinois | 60612 | — |
| Children's Hospital of Boston | Boston | Massachusetts | 022105 | — |
| University of Minnesota, Masonic Clinical Research Unit, Clinical and Translational Science Institute | Minneapolis | Minnesota | 55455 | — |
| Mount Sinai Medical Center | New York | New York | 10029 | — |
| The Hemophilia Center, Oregon Health and Science University | Portland | Oregon | 97239 | — |
| Medical University of South Carolina | Charleston | South Carolina | 29425 | — |
| Gulf States Hemophilia and Thrombosis Center | Houston | Texas | 77030 | — |
| Bloodworks Northwest | Seattle | Washington | 98104 | — |
| BloodCenter of Wisconsin | Milwaukee | Wisconsin | 53226 | — |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT01687608, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted Mar 20, 2026 · Synced Oct 25, 2026
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Open the official record
The complete public registry record, listed eligibility criteria, and available contact information for NCT01687608 live on ClinicalTrials.gov.