ClinicalTrials.gov record
Completed Phase 3 Interventional Results available

Efficacy and Safety Study of Deferiprone in Patients With Pantothenate Kinase-associated Neurodegeneration (PKAN)

ClinicalTrials.gov ID: NCT01741532

Public ClinicalTrials.gov record NCT01741532. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 12, 2026, 10:08 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Randomized, Double-blind, Placebo-controlled Trial of Deferiprone in Patients With Pantothenate Kinase-associated Neurodegeneration (PKAN)

Study identification

NCT ID
NCT01741532
Recruitment status
Completed
Study type
Interventional
Phase
Phase 3
Lead sponsor
ApoPharma
Industry
Enrollment
89 participants

Conditions and interventions

Interventions

  • Deferiprone oral solution Drug
  • Placebo Drug

Drug

Eligibility (public fields only)

Age range
4 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Dec 12, 2012
Primary completion
Oct 20, 2016
Completion
Jan 10, 2017
Last update posted
Jul 4, 2019

2012 – 2017

United States locations

U.S. sites
1
U.S. states
1
U.S. cities
1
Facility City State ZIP Site status
Children's Hospital & Research Center at Oakland Oakland California 94609

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 3 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT01741532, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Jul 4, 2019 · Synced May 12, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT01741532 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →