Allogeneic Hematopoietic Stem Cell Transplant for GATA2 Mutations
Public ClinicalTrials.gov record NCT01861106. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Official title
Allogeneic Hematopoietic Stem Cell Transplant for Patients With Mutations in GATA2 or the MonoMAC Syndrome
Study identification
- NCT ID
- NCT01861106
- Recruitment status
- Recruiting
- Study type
- Interventional
- Phase
- Phase 2
- Lead sponsor
- National Cancer Institute (NCI)
- NIH
- Enrollment
- 144 participants
Conditions and interventions
Conditions
Interventions
- Allogeneic HSCT Procedure
- Busulfan (Busulfex) Drug
- Busulfan Test dose Drug
- Cyclophosphamide (CTX, Cytoxan) Drug
- Equine Anti-Thymocyte Globulin Biological
- Fludarabine (Fludara, Berlex Laboratories) Drug
- Mycophenolate mofetil (MMF) Drug
- Tacrolimus Drug
- Total Body Irradiation (TBI) Procedure
Procedure · Drug · Biological
Eligibility (public fields only)
- Age range
- 6 Years to 70 Years
- Sex
- All
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Jul 23, 2013
- Primary completion
- Dec 30, 2027
- Completion
- Dec 30, 2028
- Last update posted
- May 6, 2026
2013 – 2028
United States locations
- U.S. sites
- 1
- U.S. states
- 1
- U.S. cities
- 1
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| National Institutes of Health Clinical Center | Bethesda | Maryland | 20892 | Recruiting |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT01861106, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted May 6, 2026 · Synced May 9, 2026
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Open the official record
The complete protocol, eligibility criteria, and contact information for NCT01861106 live on ClinicalTrials.gov.