ClinicalTrials.gov record
Active, not recruiting Phase 1Phase 2 Interventional

Pegtibatinase As an Enzyme Therapy for Patients with Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (COMPOSE)

ClinicalTrials.gov ID: NCT03406611

Public ClinicalTrials.gov record NCT03406611. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 21, 2026, 1:01 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Double Blind, Randomized, Placebo-controlled, Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Effects on Clinical Outcomes of Pegtibatinase (TVT-058), Administered Subcutaneously in Patients with Cystathionine Beta-Synthase Deficient Homocystinuria (COMPOSE)

Study identification

NCT ID
NCT03406611
Recruitment status
Active, not recruiting
Study type
Interventional
Phase
Phase 1, Phase 2
Lead sponsor
Travere Therapeutics, Inc.
Industry
Enrollment
32 participants

Conditions and interventions

Conditions

Interventions

  • Pegtibatinase Drug
  • Placebo Drug

Drug

Eligibility (public fields only)

Age range
12 Years to 65 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jan 21, 2019
Primary completion
May 31, 2026
Completion
Nov 30, 2026
Last update posted
Nov 21, 2024

2019 – 2026

United States locations

U.S. sites
8
U.S. states
8
U.S. cities
8
Facility City State ZIP Site status
Travere Investigational Site - Virtual Site Culver City California 90230
Travere Investigational Site Aurora Colorado 80045
Travere Investigational Site Miami Florida 33136
Travere Investigational Site Indianapolis Indiana 46202
Travere Investigational Site Portland Maine 04102
Travere Investigational Site Boston Massachusetts 02115
Travere Investigational Site New York New York 10029
Travere Investigational Site Philadelphia Pennsylvania 19104

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03406611, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Nov 21, 2024 · Synced May 21, 2026

Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.

Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03406611 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →