ClinicalTrials.gov record
Approved For Marketing No phase listed Expanded access

A Maralixibat Expanded Access Program for Patients With Cholestatic Pruritus Associated With Alagille Syndrome (ALGS)

ClinicalTrials.gov ID: NCT04530994

Public ClinicalTrials.gov record NCT04530994. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 19, 2026, 8:11 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Maralixibat Expanded Access Program for Patients With Cholestatic Pruritus Associated With Alagille Syndrome

Study identification

NCT ID
NCT04530994
Recruitment status
Approved For Marketing
Study type
Expanded access
Phase
Not listed
Lead sponsor
Mirum Pharmaceuticals, Inc.
Industry
Enrollment
Not listed

Conditions and interventions

Interventions

  • maralixibat Drug

Drug

Eligibility (public fields only)

Age range
12 Months and older
Sex
All
Healthy volunteers
Not listed

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Not listed
Primary completion
Not listed
Completion
Not listed
Last update posted
Oct 19, 2021

United States locations

U.S. sites
14
U.S. states
12
U.S. cities
14
Facility City State ZIP Site status
University of California, Los Angeles Los Angeles California 90095
Stanford University Redwood City California 94063
University of California San Francisco San Francisco California 94158
Georgetown University Washington D.C. District of Columbia 20007
Advent Health Orlando Florida 32804
Children's Healthcare of Atlanta/Emory University Atlanta Georgia 30329
Ann & Robert H. Lurie Children's Hospital Chicago Illinois 60611
Ochsner Clinic Foundation New Orleans Louisiana 70121
University of Minnesota Minneapolis Minnesota 55455
The Children's Hospital at Montefiore New York New York 10467
University of Oklahoma Oklahoma City Oklahoma 73104
Baylor College of Medicine Houston Texas 77030
University of Virginia Charlottesville Virginia 22903
Medical College of Wisconsin Milwaukee Wisconsin 53226

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT04530994, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Oct 19, 2021 · Synced May 19, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT04530994 live on ClinicalTrials.gov.

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