ClinicalTrials.gov record
Active, not recruiting Phase 3 Interventional Results available

Global Safety and Efficacy Registration Study of Crinecerfont in Pediatric Participants With Classic Congenital Adrenal Hyperplasia (CAHtalyst Pediatric Study)

ClinicalTrials.gov ID: NCT04806451

Public ClinicalTrials.gov record NCT04806451. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 8, 2026, 5:05 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Safety and Efficacy of Crinecerfont (NBI-74788) in Pediatric Subjects With Classic Congenital Adrenal Hyperplasia, Followed by Open-Label Treatment

Study identification

NCT ID
NCT04806451
Recruitment status
Active, not recruiting
Study type
Interventional
Phase
Phase 3
Lead sponsor
Neurocrine Biosciences
Industry
Enrollment
103 participants

Conditions and interventions

Interventions

  • Crinecerfont Drug
  • Placebo Drug

Drug

Eligibility (public fields only)

Age range
2 Years to 17 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jun 24, 2021
Primary completion
Mar 9, 2023
Completion
Jul 31, 2027
Last update posted
Feb 4, 2025

2021 – 2027

United States locations

U.S. sites
22
U.S. states
16
U.S. cities
22
Facility City State ZIP Site status
Neurocrine Clinical Site Birmingham Alabama 35233
Neurocrine Clinical Site Los Angeles California 90027
Neurocrine Clinical Site Orange California 92868
Neurocrine Clinical Site San Diego California 92123
Neurocrine Clinical Site San Francisco California 94158
Neurocrine Clinical Site Aurora Colorado 80045
Neurocrine Clinical Site Hartford Connecticut 06106
Neurocrine Clinical Site Washington D.C. District of Columbia 20010
Neurocrine Clinical Site Atlanta Georgia 30329
Neurocrine Clinical Site Indianapolis Indiana 46202
Neurocrine Clinical Site Boston Massachusetts 02115
Neurocrine Clinical Site Ann Arbor Michigan 48109
Neurocrine Clinical Site Minneapolis Minnesota 55454
Neurocrine Clinical site St Louis Missouri 63104
Neurocrine Clinical Site New Hyde Park New York 11040
Neurocrine Clinical Site New York New York 10065
Neurocrine Clinical Site Oklahoma City Oklahoma 73104
Neurocrine Clinical Site Tulsa Oklahoma 74135
Neurocrine Clinical Site Philadelphia Pennsylvania 19104
Neurocrine Clinical Site Pittsburgh Pennsylvania 15224
Neurocrine Clinical Site Dallas Texas 75235
Neurocrine Clinical Site Seattle Washington 98105

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 24 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT04806451, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Feb 4, 2025 · Synced May 8, 2026

Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.

Open the official record

The complete protocol, eligibility criteria, and contact information for NCT04806451 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →