ClinicalTrials.gov record
Recruiting Phase 1Phase 2 Interventional

A Phase 1/2 Study of Enzomenib (DSP-5336) in Patients With Acute Leukemia (Horizen-1)

ClinicalTrials.gov ID: NCT04988555

Public ClinicalTrials.gov record NCT04988555. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Apr 29, 2026, 9:07 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 1/2, Open-Label, Dose-Escalation, Dose-Expansion Study of Enzomenib (DSP-5336) in Patients With Acute Leukemia and Other Selected Hematologic Malignancies, With and Without Mixed Lineage Leukemia (MLL) Rearrangement or Nucleophosmin 1 (NPM1) Mutation (Horizen-1)

Study identification

NCT ID
NCT04988555
Recruitment status
Recruiting
Study type
Interventional
Phase
Phase 1, Phase 2
Lead sponsor
Sumitomo Pharma America, Inc.
Industry
Enrollment
606 participants

Conditions and interventions

Interventions

  • Azacitidine (AZA) Drug
  • Enzomenib Drug
  • Gilteritinib Drug
  • Intensive chemotherapy with 7 + 3 Drug
  • Venetoclax Drug
  • azoles Drug

Drug

Eligibility (public fields only)

Age range
12 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Feb 27, 2022
Primary completion
Jun 29, 2027
Completion
Dec 30, 2027
Last update posted
Mar 23, 2026

2022 – 2027

United States locations

U.S. sites
33
U.S. states
18
U.S. cities
27
Facility City State ZIP Site status
Hoag Family Cancer Center Newport Beach California 92663 Recruiting
Stanford University Palo Alto California 94304 Not yet recruiting
Colorado Blood Cancer Institute Denver Colorado 80218 Recruiting
Georgetown Lombardi Comprehensive Cancer Center Washington D.C. District of Columbia 20007 Not yet recruiting
University of Miami Miami Florida 33136 Recruiting
Miami Cancer Institute Miami Florida 33176 Not yet recruiting
Moffitt Cancer Center Tampa Florida 33612 Not yet recruiting
Northwestern Chicago Illinois 60611 Recruiting
Sibley Memorial Hospital Baltimore Maryland 20016 Recruiting
University of Maryland Baltimore Maryland 21201 Recruiting
Johns Hopkins Main Center Baltimore Maryland 21287 Recruiting
Tufts University Boston Massachusetts 02111 Withdrawn
Massachusetts General Hospital Boston Massachusetts 02114 Recruiting
Atlantic Health Morristown New Jersey 07960 Recruiting
Rutgers Cancer Institute of New Jersey New Brunswick New Jersey 08901 Recruiting
Roswell Park Comprehensive Cancer Center Buffalo New York 14203 Recruiting
Mount Sinai Hospital New York New York 10029 Completed
Columbia University New York New York 10032 Completed
UNC Hospital Chapel Hill North Carolina 27514 Recruiting
Duke University Durham North Carolina 27705 Recruiting
Atrium Wake Forest Baptist Medical Center Winston-Salem North Carolina 27157 Recruiting
The Ohio State University Comprehensive Cancer Center Columbus Ohio 43210 Recruiting
Oncology Associates of Oregon Eugene Oregon 97401 Recruiting
Sidney Kimmel Comprehensive Cancer Center Philadelphia Pennsylvania 19107 Recruiting
Allegheny Health Network Pittsburgh Pennsylvania 15224 Recruiting
Medical University of South Carolina Charleston South Carolina 29425 Recruiting
TriStar Centennial Medical Center Nashville Tennessee 37203 Recruiting
MDACC Houston Texas 77030 Recruiting
Huntsman Cancer Institute Salt Lake City Utah 84112 Recruiting
Intermountain Healthcare Salt Lake City Utah 84143 Recruiting
University of Virginia Charlottesville Virginia 22908 Recruiting
Virginia Cancer Specialists Fairfax Virginia 22031 Recruiting
Virginia Oncology Associates Norfolk Virginia 23502 Recruiting

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 71 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT04988555, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Mar 23, 2026 · Synced Apr 29, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT04988555 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →