ClinicalTrials.gov record
Enrolling by invitation Phase 3 Interventional

An Extension Study to Assess Long-Term Safety of Eplontersen in Adults With Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)

ClinicalTrials.gov ID: NCT05667493

Public ClinicalTrials.gov record NCT05667493. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Apr 22, 2026, 8:29 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

An Open-Label Extension Study to Assess the Long-Term Safety of Eplontersen (ION-682884) in Patients With Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)

Study identification

NCT ID
NCT05667493
Recruitment status
Enrolling by invitation
Study type
Interventional
Phase
Phase 3
Lead sponsor
Ionis Pharmaceuticals, Inc.
Industry
Enrollment
1,400 participants

Conditions and interventions

Interventions

  • Eplontersen Drug

Drug

Eligibility (public fields only)

Age range
18 Years and older
Sex
All
Healthy volunteers
Not listed

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Nov 29, 2022
Primary completion
Jul 31, 2029
Completion
Jul 31, 2029
Last update posted
Apr 16, 2026

2022 – 2029

United States locations

U.S. sites
46
U.S. states
26
U.S. cities
38
Facility City State ZIP Site status
Mayo Clinic Scottsdale Arizona 85259
Cedars-Sinai Medical Center Beverly Hills California 90211
Altman Clinical and Translational Research Institute - Center for Clinical Research La Jolla California 92037
University Of California San Francisco Urology Practice San Francisco California 94143
Stanford University (Leland Stanford Junior University) Stanford California 94305
University of Colorado Hospital - Anschutz Medical Campus Aurora Colorado 80045
MedStar Washington Hospital Center Washington D.C. District of Columbia 20010
The George Washington Medical Faculty Associates - Foggy Bottom North Pavilion Washington D.C. District of Columbia 20037
Cleveland Clinic Florida Weston Florida 33331
Piedmont Heart of Fayetteville Atlanta Georgia 30309
Emory Heart and Vascular Center - Emory Clifton Campus Atlanta Georgia 30322
Piedmont Atlanta Hospital Fayetteville Georgia 30214
Northwestern University Chicago Illinois 60611
Loyola University Medical Center Maywood Illinois 60153
Indiana University Health University Hospital Indianapolis Indiana 46202
University of Kansas Medical Center (KUMC) Kansas City Kansas 66160
University of Kansas Medical Center Kansas City Kansas 66160
University of Maryland Medical Center Baltimore Maryland 21201
Massachusetts General Hospital Boston Massachusetts 02114
Brigham and Women's Hospital Boston Massachusetts 02115
Boston University School of Medicine Boston Massachusetts 02118
Henry Ford Health System Detroit Michigan 48202
Allina Health Minneapolis Heart Institute - Abbott Northwestern's Heart Hospital Minneapolis Minnesota 55407
Mayo Clinic Rochester Minnesota 55905
Saint Luke's Hospital of Kansas City Kansas City Missouri 64111
Barnes-Jewish Hospital St Louis Missouri 63110
New York University Langone Cardiology Associates New York New York 10016
Weill Cornell Medicine Cardiology New York New York 10021
Columbia University Irving Medical Center New York New York 10034
University of North Carolina at Chapel Hill Chapel Hill North Carolina 27599
Duke University Medical Center Durham North Carolina 27710
Carl and Edyth Lindner Research Center at The Christ Hospital Cincinnati Ohio 45219
University Hospitals Cleveland Medical Center Cleveland Ohio 44106
Cleveland Clinic Main Campus Cleveland Ohio 44195
The Ohio State University College of Medicine Columbus Ohio 43210
Oregon Health and Science University Portland Oregon 97239
Lancaster General Hospital Lancaster Pennsylvania 17602
Penn Presbyterian Medical Center Philadelphia Pennsylvania 19104
Medical University of South Carolina Charleston South Carolina 29425
Vanderbilt Heart and Vascular Institute Nashville Tennessee 37232
University of Texas Southwestern Medical Center Dallas Texas 75390
Houston Methodist Hospital Houston Texas 77030
University of Utah Salt Lake City Utah 84112
Virginia Commonwealth University Richmond Virginia 23298
University of Washington Seattle Washington 98195
University of Wisconsin - Madison Madison Wisconsin 53792

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 88 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT05667493, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Apr 16, 2026 · Synced Apr 22, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT05667493 live on ClinicalTrials.gov.

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