ClinicalTrials.gov record
Recruiting Phase 1Phase 2 Interventional

A Phase I/II Study of Trametinib and Azacitidine for Patients With Newly Diagnosed Juvenile Myelomonocytic Leukemia

ClinicalTrials.gov ID: NCT05849662

Public ClinicalTrials.gov record NCT05849662. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 8, 2026, 8:10 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Risk Stratified Treatment for Patients With Newly Diagnosed Juvenile Myelomonocytic Leukemia: A Phase I/II Non-randomized Study of Trametinib and Azacitidine With or Without Chemotherapy (IND #164058)

Study identification

NCT ID
NCT05849662
Recruitment status
Recruiting
Study type
Interventional
Phase
Phase 1, Phase 2
Lead sponsor
Therapeutic Advances in Childhood Leukemia Consortium
Other
Enrollment
58 participants

Conditions and interventions

Interventions

  • Azacitidine Drug
  • Cytarabine Drug
  • Fludarabine Drug
  • Trametinib Drug

Drug

Eligibility (public fields only)

Age range
1 Month to 21 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Oct 10, 2024
Primary completion
Nov 30, 2028
Completion
Nov 30, 2029
Last update posted
Apr 14, 2026

2024 – 2029

United States locations

U.S. sites
19
U.S. states
18
U.S. cities
19
Facility City State ZIP Site status
Phoenix Children's Hospital Phoenix Arizona 85016 Recruiting
Children's Hospital Los Angeles Los Angeles California 900027 Recruiting
University of California San Francisco San Francisco California 94158 Recruiting
Children's Hospital of Colorado Denver Colorado 80045 Recruiting
Children's National Medical Center Washington D.C. District of Columbia 20010 Recruiting
University of Miami Miami Florida 33136 Recruiting
Children's Hospital of Atlanta Atlanta Georgia 30322 Recruiting
Lurie Children's Hospital of Chicago Chicago Illinois 60611 Recruiting
Indiana University/Riley Hospital for Children Indianapolis Indiana 46202 Recruiting
Sidney Kimmel Cancer Center at Johns Hopkins Baltimore Maryland 21231 Recruiting
C.S. Mott Children's Hospital Ann Arbor Michigan 48109 Recruiting
Children's Mercy Hospital Kansas City Missouri 64108 Recruiting
Memorial Sloan Kettering Cancer Center New York New York 10065 Recruiting
Cincinnati Children's Hospital Medical Center Cincinnati Ohio 45229 Recruiting
Oregon Health & Science University Portland Oregon 97239 Recruiting
Children's Hospital of Philadelphia Philadelphia Pennsylvania 19104 Recruiting
St. Jude Children's Research Hospital Memphis Memphis Tennessee 38105 Recruiting
Primary Children's Hospital Salt Lake City Utah 84113 Recruiting
Seattle Children's Hospital Seattle Washington 98105 Recruiting

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT05849662, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Apr 14, 2026 · Synced May 8, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT05849662 live on ClinicalTrials.gov.

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