ClinicalTrials.gov record
Recruiting Phase 2 Interventional

A Phase 2 Trial of ALN-APP in Patients With Cerebral Amyloid Angiopathy

ClinicalTrials.gov ID: NCT06393712

Public ClinicalTrials.gov record NCT06393712. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Apr 27, 2026, 7:25 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 2, Randomized, Double-blind, Placebo-controlled Study to Evaluate the Efficacy, Safety, Tolerability, and Pharmacodynamics of Intrathecally Administered ALN-APP in Patients With Cerebral Amyloid Angiopathy (CAA)

Study identification

NCT ID
NCT06393712
Recruitment status
Recruiting
Study type
Interventional
Phase
Phase 2
Lead sponsor
Alnylam Pharmaceuticals
Industry
Enrollment
200 participants

Conditions and interventions

Interventions

  • ALN-APP Drug
  • Placebo Drug

Drug

Eligibility (public fields only)

Age range
30 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
May 16, 2024
Primary completion
Aug 8, 2027
Completion
Dec 13, 2029
Last update posted
Apr 23, 2026

2024 – 2029

United States locations

U.S. sites
34
U.S. states
17
U.S. cities
30
Facility City State ZIP Site status
Clinical Trial Site Los Angeles California 90095 Active, not recruiting
Clinical Trial Site Orange California 92868 Active, not recruiting
Clinical Trial Site Palo Alto California 94304 Active, not recruiting
Clinical Trial Site Sacramento California 95816 Active, not recruiting
Clinical Trial Site San Francisco California 94114 Active, not recruiting
Clinical Trial Site Aurora Colorado 80045 Active, not recruiting
Clinical Trial Site New Haven Connecticut 06510 Active, not recruiting
Clinical Trial Site Gainesville Florida 32608 Active, not recruiting
Clinical Trial Site Jacksonville Florida 32224 Active, not recruiting
Clinical Trial Site Maitland Florida 32751 Active, not recruiting
Clinical Trial Site Naples Florida 34105 Active, not recruiting
Clinical Trial Site Chicago Illinois 60612 Active, not recruiting
Clinical Trial Site Lexington Kentucky 40504 Active, not recruiting
Clinical Trial Site New Orleans Louisiana 70121 Active, not recruiting
Clinical Trial Site Boston Massachusetts 02114 Active, not recruiting
Clinical Trial Site Plymouth Massachusetts 02360 Active, not recruiting
Clinical Trial Site Rochester Minnesota 55905 Active, not recruiting
Clinical Trial Site St Louis Missouri 63110 Active, not recruiting
Clinical Trial Site Hackensack New Jersey 07601 Active, not recruiting
Clinical Trial Site New York New York 10016 Active, not recruiting
Clinical Trial Site New York New York 10029 Active, not recruiting
Clinical Trial Site New York New York 10032 Active, not recruiting
Clinical Trial Site New York New York 10065 Active, not recruiting
Clinical Trial Site Durham North Carolina 27705 Active, not recruiting
Clinical Trial Site Canton Ohio 44718 Active, not recruiting
Clinical Trial Site Cleveland Ohio 44195 Active, not recruiting
Clinical Trial Site Abington Pennsylvania 19001 Active, not recruiting
Clinical Trial Site Philadelphia Pennsylvania 19104 Active, not recruiting
Clinical Trial Site Pittsburgh Pennsylvania 15213 Active, not recruiting
Clinical Trial Site Dallas Texas 75243 Active, not recruiting
Clinical Trial Site Dallas Texas 75390 Active, not recruiting
Clinical Trial Site Houston Texas 77030 Active, not recruiting
Clinical Trial Site San Antonio Texas 78229 Active, not recruiting
Clinical Trial Site Seattle Washington 98104 Active, not recruiting

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 23 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT06393712, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Apr 23, 2026 · Synced Apr 27, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT06393712 live on ClinicalTrials.gov.

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