An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia

ClinicalTrials.gov ID: NCT06447025

Public ClinicalTrials.gov record NCT06447025. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

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ClinicalTrials.gov public records Last synced May 20, 2026, 11:47 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

An Open-Label Extension Study to Assess the Long-Term Safety, Efficacy, Pharmacodynamics, Pharmacokinetics, and Tolerability of Subcutaneous CTI-1601 in Subjects With Friedreich's Ataxia

Study identification

NCT ID: NCT06447025
Recruitment status: Recruiting
Study type: Interventional
Phase: Phase 2
Lead sponsor: Larimar Therapeutics, Inc.; Industry
Enrollment: 85 participants

Conditions and interventions

Conditions

Friedreich Ataxia

Interventions

CTI-1601 Drug

Drug

Eligibility (public fields only)

Age range: 2 Years to 60 Years
Sex: All
Healthy volunteers: Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date: Jan 24, 2024
Primary completion: Dec 31, 2026
Completion: Dec 31, 2026
Last update posted: May 12, 2026

2024 – 2027

United States locations

U.S. sites: 8
U.S. states: 7
U.S. cities: 8

Facility	City	State	ZIP	Site status
University of California Los Angeles	Los Angeles	California	90095	Recruiting
Fixel Institute for Neurological Disease, University of Florida Health	Gainesville	Florida	32608	Active, not recruiting
Morsani Center for Advanced Health Care, University of South Florida Health	Tampa	Florida	33612	Recruiting
University of Iowa	Iowa City	Iowa	52242	Recruiting
Uncommon Cures	Chevy Chase	Maryland	20815	Recruiting
Clinilabs Drug Development, Corp.	Eatontown	New Jersey	07724	Recruiting
Ohio State University United States	Columbus	Ohio	43210	Active, not recruiting
Children's Hospital of the University of Pennsylvania (CHOP)	Philadelphia	Pennsylvania	19104	Recruiting

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows: Public field values for ClinicalTrials.gov record NCT06447025, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do: No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from: Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh: Last update posted May 12, 2026 · Synced May 20, 2026

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The complete protocol, eligibility criteria, and contact information for NCT06447025 live on ClinicalTrials.gov.

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