ClinicalTrials.gov record
Recruiting No phase listed Observational

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

ClinicalTrials.gov ID: NCT06564974

Public ClinicalTrials.gov record NCT06564974. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 6, 2026, 8:34 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy [SUpplemental Patient dMd assessMents Investigating ouTcomes (SUMMIT)]

Study identification

NCT ID
NCT06564974
Recruitment status
Recruiting
Study type
Observational
Phase
Not listed
Lead sponsor
Catalyst Pharmaceuticals, Inc.
Industry
Enrollment
250 participants

Conditions and interventions

Interventions

  • Vamorolone Drug

Drug

Eligibility (public fields only)

Age range
2 Years and older
Sex
Male
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Sep 24, 2024
Primary completion
Jan 31, 2032
Completion
Jan 31, 2032
Last update posted
Feb 26, 2026

2024 – 2032

United States locations

U.S. sites
25
U.S. states
16
U.S. cities
25
Facility City State ZIP Site status
Phoenix Children's Hospital Phoenix Arizona 85016 Recruiting
Arkansas Childrens Hospital Little Rock Arkansas 72202 Recruiting
Children's Hospital Los Angeles Los Angeles California 90027 Not yet recruiting
Stanford University Palo Alto California 94305 Not yet recruiting
University of California, Davis Sacramento California 95817 Not yet recruiting
University of Florida Clinical and Translational Science Institue Gainesville Florida 32610 Not yet recruiting
Nicklaus Children's Hospital Miami Florida 33155 Recruiting
Nemours Children's Hospital Orlando Florida 32827 Recruiting
Johns Hopkins All Children's Hospital St. Petersburg Florida 33701 Not yet recruiting
Lurie Children's Hospital of Chicago Chicago Illinois 60611 Recruiting
Indiana University Health - Riley Hospital for Children Indianapolis Indiana 46202 Not yet recruiting
University of Kansas Medical Center Kansas City Kansas 66205 Recruiting
University of Massachusetts Memorial Medical Center North Worcester Massachusetts 01655 Recruiting
Helen DeVos Children's Hospital Grand Rapids Michigan 49503 Recruiting
Atrium Health Neurosciences Institute Charlotte North Carolina 28207 Recruiting
Duke University Medical Center and Childrens Health Center Durham North Carolina 27710 Recruiting
Cincinnati Children's Hospital Medical Center Cincinnati Ohio 45229 Recruiting
Penn State Milton S. Hershey Medical Center- Penn State Hershey Neuroscience Institute Hershey Pennsylvania 17033 Recruiting
Children's Hospital of Philadelphia (CHOP) Philadelphia Pennsylvania 19104 Recruiting
University of Texas Southwestern Medical Center Dallas Texas 75235 Recruiting
Neurology Rare Disease Center - Neurology & Neuromuscular Care Center Denton Texas 76208 Recruiting
The University of Texas Health Science Center at San Antonio San Antonio Texas 78229 Recruiting
University of Virginia Health System (UVAHS) - Pediatric Neuromuscular Center Charlottesville Virginia 22903 Recruiting
Seattle Children's Hospital Seattle Washington 98105 Recruiting
Children's Wisconsin Milwaukee Wisconsin 53226 Not yet recruiting

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 2 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT06564974, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Feb 26, 2026 · Synced May 6, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT06564974 live on ClinicalTrials.gov.

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