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Recruiting Phase 2 Interventional

Study to Evaluate Efficacy and Safety of ONL1204 in Patients With GA Associated With AMD

ClinicalTrials.gov ID: NCT06659445

Public ClinicalTrials.gov record NCT06659445. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Sep 9, 2026, 7:44 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 2 Multicenter, Randomized, Double-masked, Sham-controlled, Reference-arm Study to Evaluate Efficacy and Safety of ONL1204 in Patients With Geographic Atrophy (GA) Associated With Age-related Macular Degeneration (AMD)

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

The purpose of this study is to collect efficacy and safety information of intravitreal injection for 3 experimental arms, including 2 dose levels of ONL1204 and 2 treatment frequencies in patients with GA associated with AMD. GA associated with AMD is one of the world's leading causes of visual disability and legal blindness globally. Associated with aging, cigarette smoking, obesity, diets low in certain nutrients, a lifestyle related to cardiac risk, and a growing list of genetic factors, AMD is becoming an increasingly prevalent public health concern, especially as the global population ages. ONL1204 is a first-in-class inhibitor of fragment apoptosis stimulator receptor-mediated cell death that has demonstrated protection of multiple retinal cell types in numerous preclinical models of retinal disease, including models of dry AMD.

Study identification

NCT ID
NCT06659445
Recruitment status
Recruiting
Study type
Interventional
Phase
Phase 2
Lead sponsor
ONL Therapeutics
Industry
Enrollment
324 participants

Conditions and interventions

Eligibility (public fields only)

Age range
55 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Oct 27, 2025
Primary completion
Oct 31, 2028
Completion
Oct 31, 2028
Last update posted
Aug 25, 2026

2025 – 2028

United States locations

U.S. sites
53
U.S. states
22
U.S. cities
51
Facility City State ZIP Site status
Associated Retina Consultants Gilbert Arizona 85297 Recruiting
Associated Retina Consultants Phoenix Arizona 85020 Recruiting
California Retina Consultants Bakersfield California 93309 Recruiting
Retina-Vitreous Associates Medical Group Beverly Hills California 90211 Recruiting
Macula and Retina Institute Glendale California 91203 Recruiting
Salehi Retina Institute, dba Retina Associates of Southern California Huntington Beach California 92647 Recruiting
Desert Retina Consultants Palm Desert California 92211 Recruiting
Retinal Consultants Medical Group Sacramento California 95841 Recruiting
Bay Area Retina Associates Walnut Creek California 94598 Recruiting
Retina Consultants of Southern Colorado Colorado Springs Colorado 80909-1183 Recruiting
Retina Group of New England Waterford Connecticut 06385 Recruiting
Florida Retina Institute Orlando Florida 32806 Recruiting
Retina Specialty Institute Pensacola Florida 32503 Recruiting
Retina Group of Florida Sarasota Florida 34232 Recruiting
Retina Associates of Florida, LLC Tampa Florida 33609-4614 Recruiting
Northwestern Medical Group Chicago Illinois 60611 Recruiting
The University of Chicago Medicine Duchossois Center for Advanced Medicine Chicago Illinois 60637 Recruiting
Retina Associates, Ltd. Elmhurst Illinois 60126 Recruiting
Illinois Retina Associates, S.C. Oak Park Illinois 60304 Recruiting
Retina Partners Midwest, P.C. Carmel Indiana 46032 Recruiting
Retina Specialists Towson Maryland 21204 Recruiting
Retina Research Institute at New England Retina Consultants Springfield Massachusetts 01107 Recruiting
University of Michigan Kellogg Eye Center Ann Arbor Michigan 48105 Recruiting
Associated Retinal Consultants, P.C. Royal Oak Michigan 48073 Recruiting
Associated Retinal Consultants, P.C. Traverse City Michigan 49686 Recruiting
Mayo Clinic Rochester Minnesota 55905 Recruiting
The Retina Institute St Louis Missouri 63128 Recruiting
Sierra Eye Associates Reno Nevada 89502 Recruiting
Retina Vitreous Surgeons of CNY, PC Liverpool New York 13088 Recruiting
Ophthalmic Consultants of Long Island Oceanside New York 11572 Recruiting
Retina Associates of Western NY Rochester New York 14620 Recruiting
Long Island Vitreoretinal Consultants Westbury New York 11590 Recruiting
North Carolina Retina Associates Cary North Carolina 27511 Recruiting
Duke Eye Center Durham North Carolina 27710 Recruiting
North Carolina Retina Associates Greenville North Carolina 27834 Recruiting
North Carolina Retina Associates, S.C. Wake Forest North Carolina 27587 Recruiting
Cleveland Clinic Foundation-Cole Eye Institute Cleveland Ohio 44195 Recruiting
Erie Retina Research, LLC (Clinic) Erie Pennsylvania 16505 Recruiting
Charleston Neuroscience Institute Mt. Pleasant South Carolina 29464 Recruiting
Palmetto Retina Center West Columbia South Carolina 29169 Recruiting
Vanderbilt Eye Institute Nashville Tennessee 37232 Recruiting
Austin Retina Associates Austin Texas 78705 Recruiting
Retina Consultants of Texas Beaumont Texas 77707 Recruiting
Retina Consultants of Texas Bellaire Texas 77401 Recruiting
Retina Consultants of Texas Katy Texas 77494 Recruiting
Valley Retina Institute, P.A. McAllen Texas 78503 Recruiting
Retina Associates of South Texas, PA San Antonio Texas 78240 Recruiting
Retina Consultants of Texas San Antonio Texas 78240 Recruiting
Retina Center of Texas Southlake Texas 76092 Recruiting
Retina Consultants of Texas The Woodlands Texas 77384 Recruiting
Piedmont Eye Center Lynchburg Virginia 24502 Recruiting
Pacific Northwest Retina Bellevue Washington 98004 Recruiting
Pacific Northwest Retina, PLLC Silverdale Washington 98383 Recruiting

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 64 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT06659445, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Aug 25, 2026 · Synced Sep 9, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT06659445 live on ClinicalTrials.gov.

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