A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)
Public ClinicalTrials.gov record NCT06817382. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Official title
A Phase 1, Multicenter, Open-label Study to Investigate the Safety and Biodistribution of a Single Intrathecal Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (The ASCEND Study)
Study identification
- NCT ID
- NCT06817382
- Recruitment status
- Recruiting
- Study type
- Interventional
- Phase
- Phase 1
- Lead sponsor
- Insmed Gene Therapy LLC
- Industry
- Enrollment
- 12 participants
Conditions and interventions
Conditions
Interventions
- INS1201 Genetic
Genetic
Eligibility (public fields only)
- Age range
- 2 Years to 4 Years
- Sex
- Male
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Jul 21, 2025
- Primary completion
- Jan 30, 2028
- Completion
- Mar 30, 2028
- Last update posted
- Apr 28, 2026
2025 – 2028
United States locations
- U.S. sites
- 10
- U.S. states
- 7
- U.S. cities
- 10
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| USA012 | Little Rock | Arkansas | 72202 | Recruiting |
| USA010 | Davis | California | 95616 | Recruiting |
| USA009 | Los Angeles | California | 90095 | Recruiting |
| USA002 | Palo Alto | California | 94070 | Recruiting |
| USA005 | San Diego | California | 93123 | Recruiting |
| Rare Disease Research (USA004) | Atlanta | Georgia | 30329 | Recruiting |
| USA008 | Rochester | New York | 14642 | Recruiting |
| USA006 | Columbus | Ohio | 43205 | Recruiting |
| USA001 | Memphis | Tennessee | 38105 | Recruiting |
| USA015 | Norfolk | Virginia | 23507 | Recruiting |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT06817382, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted Apr 28, 2026 · Synced May 10, 2026
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Open the official record
The complete protocol, eligibility criteria, and contact information for NCT06817382 live on ClinicalTrials.gov.