Independent directory Public ClinicalTrials.gov records United States
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ClinicalTrials.gov public records Last synced Jun 25, 2026, 2:41 PM EDT

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Showing 1–3 of 3 matching trials from the live ClinicalTrials.gov search.
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Conditions
LAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)
Interventions
Not listed
Lead sponsor
Cure CMD
Other
Eligibility
Not listed
Healthy volunteers
Healthy volunteers not accepted
Timeline
2013 – 2014
U.S. locations
1
States / cities
San Pedro, California
Conditions
Merosin Deficient Congenital Muscular Dystrophy
Interventions
Not listed
Lead sponsor
Prothelia, Inc.
Industry
Eligibility
2 Years to 21 Years
Enrollment
75 participants
Healthy volunteers
Healthy volunteers not accepted
Timeline
2020 – 2021
U.S. locations
1
States / cities
Lakewood, California
Conditions
LAMA2-MD \(Merosin Deficient Congenital Muscular Dystrophy, MDC1A\)
Interventions
Not listed
Lead sponsor
Nationwide Children's Hospital
Other
Eligibility
Up to 5 Years
Enrollment
44 participants
Healthy volunteers
Healthy volunteers not accepted
Timeline
2025 – 2028
U.S. locations
14
States / cities
Los Angeles, California • Stanford, California • Chicago, Illinois + 11 more