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Showing 1–3 of 3 matching trials from the live ClinicalTrials.gov search.
Completed No phase listed Observational

Myotubular Myopathy Event Study

NCT01840657
Conditions
X-linked Myotubular Myopathy
Interventions
Not listed
Lead sponsor
Cure CMD
Other
Eligibility
Male only
Enrollment
33 participants
Healthy volunteers
Healthy volunteers not accepted
Timeline
2013 – 2015
U.S. locations
1
States / cities
Torrance, California
Conditions
X-Linked Myotubular Myopathy
Interventions
ASP2957, Methylprednisolone, Prednisolone, Sirolimus
Genetic · Drug
Lead sponsor
Astellas Gene Therapies
Industry
Eligibility
Up to 36 Months · Male only
Enrollment
9 participants
Healthy volunteers
Healthy volunteers not accepted
Timeline
2025 – 2027
U.S. locations
4
States / cities
Chicago, Illinois • Boston, Massachusetts • Portland, Oregon + 1 more
Conditions
Males With X-linked Myotubular Myopathy (XLMTM)
Interventions
Non-interventional, retrospective medical chart review
Other
Lead sponsor
Astellas Gene Therapies
Industry
Eligibility
Male only
Enrollment
161 participants
Healthy volunteers
Healthy volunteers not accepted
Timeline
2014 – 2019
U.S. locations
6
States / cities
San Pedro, California • Aurora, Colorado • Gainesville, Florida + 3 more