Independent directory Public ClinicalTrials.gov records United States
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ClinicalTrials.gov public records Last synced Sep 12, 2026, 3:06 AM EDT

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Showing 1–1 of 1 matching trial from the live ClinicalTrials.gov search.
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Conditions
GNE Myopathy, Hereditary Inclusion Body Myopathy (HIBM)
Interventions
SA-ER 500 mg, SA-IR 500 mg
Drug
Lead sponsor
Ultragenyx Pharmaceutical Inc
Industry
Eligibility
18 Years to 65 Years
Enrollment
59 participants
Healthy volunteers
Healthy volunteers not accepted
Timeline
2013 – 2017
U.S. locations
3
States / cities
Los Angeles, California • St Louis, Missouri • New York, New York