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ClinicalTrials.gov public records Last synced Oct 30, 2026, 11:48 AM EDT

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Showing 1–2 of 2 matching trials from the live ClinicalTrials.gov search.
Conditions
Aspartylglucosaminuria, Aspartylglucosamidase (AGA) Deficiency
Interventions
scAAV9/AGA
Genetic
Lead sponsor
Rare Trait Hope
Other
Eligibility
4 Years to 45 Years
Enrollment
9 participants
Healthy volunteers
Healthy volunteers not accepted
Timeline
2026 – 2032
U.S. locations
1
States / cities
Shreveport, Louisiana
Recruiting No phase listed Observational

AGU Registry and NHS

NCT07903402
Conditions
Aspartylglucosaminuria, Aspartylglucosamidase (AGA) Deficiency
Interventions
Not listed
Lead sponsor
Rare Trait Hope
Other
Eligibility
Not listed
Enrollment
300 participants
Healthy volunteers
Healthy volunteers not accepted
Timeline
2024 – 2036
U.S. locations
1
States / cities
New Orleans, Louisiana