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Completed Phase 1Phase 2 Interventional Results available

Efficacy and Safety Study of Genetically Targeted Enzyme Replacement Therapy for Advanced Heart Failure

ClinicalTrials.gov ID: NCT00454818

Public ClinicalTrials.gov record NCT00454818. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jul 22, 2026, 9:06 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 1/2 Trial of Intracoronary Administration of MYDICAR® (AAV1/SERCA2a) in Subjects With Heart Failure in Two Stages (Open-Label, Sequential Dose-Escalation Cohorts and Randomized, Double-Blind, Placebo-Controlled, Parallel Cohorts)

Study identification

NCT ID
NCT00454818
Recruitment status
Completed
Study type
Interventional
Phase
Phase 1, Phase 2
Lead sponsor
Celladon Corporation
Industry
Enrollment
51 participants

Conditions and interventions

Interventions

  • MYDICAR Phase 1 (Open-label, Serial Dose-Escalation Study) Genetic
  • Placebo Infusion Procedure
  • MYDICAR Phase 2 (Placebo-controlled, Randomized Study) Genetic

Genetic · Procedure

Eligibility (public fields only)

Age range
18 Years to 75 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Feb 28, 2007
Primary completion
Jul 31, 2010
Completion
Jul 31, 2012
Last update posted
Aug 19, 2014

2007 – 2012

United States locations

U.S. sites
22
U.S. states
14
U.S. cities
18
Facility City State ZIP Site status
University of California at San Diego Medical Center San Diego California 92103
San Diego Cardiac Center San Diego California 92123
Shands Hospital at University of Florida Gainesville Florida 32608
Northwestern University Chicago Illinois 60611
University of Chicago Medical Center Chicago Illinois 60637
Mid America Heart Institute, Saint Luke's Hospital Kansas City Missouri 64111
St. Louis University Hospital St Louis Missouri 63110
University of Medicine and Dentistry of New Jersey Newark New Jersey 07101
Mount Sinai Medical Center New York New York 10029
Columbia University Hospital New York New York 10032
Wake Forest University Winston-Salem North Carolina 27157
University of Cincinnati Cincinnati Ohio 45267
MetroHealth Medical Center Cleveland Ohio 44109
Cleveland Clinic Foundation Cleveland Ohio 44195
Oregon Health and Science University Portland Oregon 97239
Hospital of the University of Pennsylvania Philadelphia Pennsylvania 19104
University of Pittsburgh Medical Center, Presbyterian-Shadyside Hospital Pittsburgh Pennsylvania 15213
Tennessee Center for Clinical Trials & Harton Regional Medical Center Tullahoma Tennessee 37388
Cardiopulmonary Research Science and Technology Institute, Medical City Dallas Hospital Dallas Texas 75230
Methodist Hospital Houston Texas 77030
Intermountain Medical Center Murray Utah 84157
University of Wisconsin Madison Wisconsin 53792

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT00454818, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Aug 19, 2014 · Synced Jul 22, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT00454818 live on ClinicalTrials.gov.

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