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Completed Phase 2 Interventional Results available

Evaluating the Safety and Effectiveness of Bone Marrow Transplants in Children With Sickle Cell Disease (BMT CTN 0601)

ClinicalTrials.gov ID: NCT00745420

Public ClinicalTrials.gov record NCT00745420. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 6, 2026, 8:37 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Unrelated Donor Reduced Intensity Bone Marrow Transplant for Children With Severe Sickle Cell Disease (BMT CTN #0601)

Study identification

NCT ID
NCT00745420
Recruitment status
Completed
Study type
Interventional
Phase
Phase 2
Lead sponsor
Medical College of Wisconsin
Other
Enrollment
30 participants

Conditions and interventions

Interventions

  • Hematopoietic Stem Cell Transplantation Biological

Biological

Eligibility (public fields only)

Age range
3 Years to 19 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jul 31, 2008
Primary completion
Jun 30, 2015
Completion
Aug 31, 2016
Last update posted
Dec 8, 2022

2008 – 2016

United States locations

U.S. sites
19
U.S. states
17
U.S. cities
19
Facility City State ZIP Site status
University of Alabama at Birmingham Birmingham Alabama 35294
Children's National Medical Center Washington D.C. District of Columbia 20010
University of Miami Miami Florida 33136
Children's Healthcare of Atlanta Atlanta Georgia 30322
Ann & Robert H. Lurie Children's Hospital of Chicago Chicago Illinois 60614
Children's Hospital of New Orleans/LSUMC CCOP New Orleans Louisiana 70118
University of Michigan Medical Center Ann Arbor Michigan 48105
University of Mississippi Medical Center Jackson Mississippi 39216
Children's Mercy Hospital and Clinics Kansas City Missouri 64108
Washington University, St. Louis Children's Hospital St Louis Missouri 63110
Cohen Children's Hospital New Hyde Park New York 11040
Columbia University Medical Center New York New York 10032
University of North Carolina Hospital at Chapel Hill Chapel Hill North Carolina 27599
University Hospitals of Cleveland Cleveland Ohio 44106
Children's Hospital of Pittsburgh Pittsburgh Pennsylvania 15213
Medical University of South Carolina Charleston South Carolina 29425
Baylor College of Medicine/The Methodist Hospital Houston Texas 77030
Virginia Commonwealth University Richmond Virginia 23298
Medical College of Wisconsin Milwaukee Wisconsin 53211

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT00745420, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Dec 8, 2022 · Synced May 6, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT00745420 live on ClinicalTrials.gov.

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