A Study of Eliglustat Tartrate (Genz-112638) in Patients With Gaucher Disease Who Have Reached Therapeutic Goals With Enzyme Replacement Therapy (ENCORE)
Public ClinicalTrials.gov record NCT00943111. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Official title
A Phase 3, Randomized, Multi-Center, Multi-National, Open-Label, Active Comparator Study to Evaluate the Efficacy and Safety of Genz-112638 in Patients With Gaucher Disease Type 1 Who Have Reached Therapeutic Goals With Enzyme Replacement Therapy (ENCORE)
Brief summary
Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.
This Phase 3 study was designed to confirm the efficacy and safety of eliglustat tartrate (Genz-112638) in participants with Gaucher disease type 1 who had reached therapeutic goals with enzyme replacement therapy (ERT).
Study identification
- NCT ID
- NCT00943111
- Recruitment status
- Completed
- Study type
- Interventional
- Phase
- Phase 3
- Enrollment
- 160 participants
Conditions and interventions
Conditions
Eligibility (public fields only)
- Age range
- 18 Years and older
- Sex
- All
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Sep 2009 (Type not available)
- Primary completion
- Nov 2012 (Actual)
- Completion
- Jun 2015 (Actual)
- Last update posted
- Nov 25, 2016
2009 – 2015
United States locations
- U.S. sites
- 17
- U.S. states
- 12
- U.S. cities
- 16
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| Tower Hematology Oncology Medical Group | Beverly Hills | California | — | — |
| UCSF MS Center | San Francisco | California | — | — |
| University of Colorado Health Science Center - Aurora | Aurora | Colorado | — | — |
| Yale University School of Medicine | New Haven | Connecticut | — | — |
| Northwest Oncology Hematology Associates PA | Coral Springs | Florida | — | — |
| Emory University Medical Genetics | Decatur | Georgia | — | — |
| Children's Memorial Hospital | Chicago | Illinois | — | — |
| University of Iowa Hospitals and Clinics | Iowa City | Iowa | — | — |
| Albany Medical Center | Albany | New York | — | — |
| North Shore University Medical Center | Manhasset | New York | 11030 | — |
| Mount Sinai School of Medicine | New York | New York | — | — |
| New York University School of Medicine | New York | New York | — | — |
| Duke University Medical Center | Durham | North Carolina | — | — |
| Cincinnati Children's Hospital Medical Center | Cincinnati | Ohio | — | — |
| Children's Hospital of Philadelphia | Philadelphia | Pennsylvania | — | — |
| University of Pittsburgh Medical Center | Pittsburgh | Pennsylvania | — | — |
| O and O Alpan LLC | Springfield | Virginia | — | — |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
Non-U.S. locations
This page focuses on the U.S. directory. The official record also lists 17 non-U.S. sites.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT00943111, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted Nov 25, 2016 · Synced Oct 21, 2026
Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.
Open the official record
The complete public registry record, listed eligibility criteria, and available contact information for NCT00943111 live on ClinicalTrials.gov.