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Completed No phase listed Observational

A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype

ClinicalTrials.gov ID: NCT01358370

Public ClinicalTrials.gov record NCT01358370. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Oct 22, 2026, 5:45 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

This is a Natural History study to characterize key aspects of the clinical course of lysosomal acid lipase (LAL) deficiency/Wolman phenotype in patients.

Study identification

NCT ID
NCT01358370
Recruitment status
Completed
Study type
Observational
Phase
Not listed
Lead sponsor
Alexion Pharmaceuticals, Inc.
Industry
Enrollment
40 participants

Conditions and interventions

Interventions

Not listed

Eligibility (public fields only)

Age range
Not listed
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Nov 2010 (Type not available)
Primary completion
Jan 2013 (Actual)
Completion
Mar 2013 (Actual)
Last update posted
Jun 27, 2016

2010 – 2013

United States locations

U.S. sites
7
U.S. states
4
U.S. cities
5
Facility City State ZIP Site status
Cedars-Siani Medical Center Los Angeles California 90095-1752 —
Stanford University Palo Alto California 94305 —
University of Minnesota Minneapolis Minnesota 55455 —
Columbia University New York New York 10027 —
Ney York Presbyterian Hosptial New York New York 10032 —
North Shore Long Island Jewish Medical Center New York New York 11040 —
Children's Hospital of Pittsburgh Pittsburgh Pennsylvania 15224 —

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 7 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT01358370, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Jun 27, 2016 · Synced Oct 22, 2026

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Open the official record

The complete public registry record, listed eligibility criteria, and available contact information for NCT01358370 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →