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Recruiting No phase listed Observational

Lysosomal Acid Lipase (LAL) Deficiency Registry

ClinicalTrials.gov ID: NCT01633489

Public ClinicalTrials.gov record NCT01633489. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jul 22, 2026, 3:41 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

An Observational Disease and Clinical Outcomes Registry of Patients With Lysosomal Acid Lipase (LAL) Deficiency

Study identification

NCT ID
NCT01633489
Recruitment status
Recruiting
Study type
Observational
Phase
Not listed
Lead sponsor
Alexion Pharmaceuticals, Inc.
Industry
Enrollment
300 participants

Conditions and interventions

Eligibility (public fields only)

Age range
Not listed
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
May 29, 2013
Primary completion
Aug 29, 2029
Completion
Aug 29, 2029
Last update posted
Mar 5, 2026

2013 – 2029

United States locations

U.S. sites
19
U.S. states
14
U.S. cities
17
Facility City State ZIP Site status
Clinical Trial Site Phoenix Arizona 85016 Recruiting
Clinical Trial Site Stanford California 94305 Recruiting
Clinical Trial Site Miramar Florida 33025 Recruiting
Clinical Trial Site Orlando Florida 32806 Recruiting
Clinical Trial Site Atlanta Georgia 30322 Recruiting
Clinical Trial Site Chicago Illinois 60611 Recruiting
Clinical Trial Site Boston Massachusetts 02115 Recruiting
Clinical Trial Site Detroit Michigan 48236 Recruiting
Clinical Trial Site Minneapolis Minnesota 55404 Recruiting
Clinical Trial Site Jackson Mississippi 39216 Recruiting
Clinical Trial Site Hackensack, NJ, 7601 New Jersey 07601 Recruiting
Clinical Trial Site New York New York 10016 Recruiting
Clinical Trial Site The Bronx New York 10467 Recruiting
Clinical Trial Site Philadelphia Pennsylvania 19104-6061 Recruiting
Clinical Trial Site Philadelphia Pennsylvania 19104 Recruiting
Clinical Trial Site Philadelphia Pennsylvania 19107 Recruiting
Clinical Trial Site Houston Texas 77030 Recruiting
Clinical Trial Site Snyder Texas 79549 Recruiting
Clinical Trial Site Tacoma Washington 98405 Recruiting

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 83 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT01633489, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Mar 5, 2026 · Synced Jul 22, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT01633489 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →