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Completed Phase 2 Interventional Results available

A Phase II Study of Oral LDE225 in Patients With Hedge-Hog (Hh)-Pathway Activated Relapsed Medulloblastoma (MB)

ClinicalTrials.gov ID: NCT01708174

Public ClinicalTrials.gov record NCT01708174. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Sep 1, 2026, 11:23 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase II, Multi-center, Open-label, Single-arm Study of the Efficacy and Safety of Oral LDE225 in Patients With Hh-pathway Activated Relapsed Medulloblastoma

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

This Phase II study evaluated the safety and efficacy of LDE225 in adult and pediatric patients with Hh-pathway activated, relapsed MB.

Study identification

NCT ID
NCT01708174
Recruitment status
Completed
Study type
Interventional
Phase
Phase 2
Lead sponsor
Novartis Pharmaceuticals
Industry
Enrollment
22 participants

Conditions and interventions

Interventions

Drug

Eligibility (public fields only)

Age range
4 Months and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
May 5, 2013
Primary completion
Oct 4, 2016
Completion
Oct 4, 2016
Last update posted
Aug 10, 2017

2013 – 2016

United States locations

U.S. sites
8
U.S. states
8
U.S. cities
8
Facility City State ZIP Site status
Ann & Robert H. Lurie Children Dept of Oncology Chicago Illinois 60611
Sidney Kimmel Comprehensive Cancer Center/Johns Hopkins Med. Dept Onc Baltimore Maryland 21231
Dana Farber Cancer Institute SC-7 Boston Massachusetts 02215
Columbia University Medical Center- New York Presbyterian Dept of Oncology New York New York 10032
Cincinnati Children's Hospital Medical Center Division of Hema/Onco. Cincinnati Ohio 45229-3039
Children's Hospital of Pittsburgh Dept of Oncology Pittsburgh Pennsylvania 15213-2583
University of Texas/MD Anderson Cancer Center SC-3 Houston Texas 77030-4009
Seattle Cancer Care Alliance Dept Oncology Seattle Washington 98105

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 33 non-U.S. sites.

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About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT01708174, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Aug 10, 2017 · Synced Sep 1, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT01708174 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →