Spinal Muscular Atrophy (SMA) Biomarkers Study in the Immediate Postnatal Period of Development
Public ClinicalTrials.gov record NCT01736553. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
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Official title
Spinal Muscular Atrophy (SMA) Biomarkers in the Immediate Postnatal Period of Development
Brief summary
Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.
Spinal muscular atrophy (SMA) is the leading genetic cause of death of infants. Strong preclinical evidence suggests that effective therapy must be delivered as early as possible to prevent progression of the disease. The primary study objective will be to identify prognostic and surrogate biomarkers of disease progression that will facilitate the execution of therapeutic SMA clinical trials in infants.
Study identification
- NCT ID
- NCT01736553
- Recruitment status
- Completed
- Study type
- Observational
- Phase
- Not listed
- Enrollment
- 53 participants
Conditions and interventions
Conditions
Interventions
Not listed
Eligibility (public fields only)
- Age range
- Up to 6 Months
- Sex
- All
- Healthy volunteers
- Accepts healthy volunteers
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Dec 2012 (Type not available)
- Primary completion
- Sep 2015 (Actual)
- Completion
- Sep 2015 (Actual)
- Last update posted
- May 4, 2018
2012 – 2015
United States locations
- U.S. sites
- 15
- U.S. states
- 12
- U.S. cities
- 15
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| University of California - Davis | Davis | California | 95616 | — |
| University of California - Los Angeles | Los Angeles | California | 90095 | — |
| Children's Hospital Colorado | Aurora | Colorado | 80045 | — |
| Children's National Medical Center | Washington D.C. | District of Columbia | 20010 | — |
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago | Illinois | 60611 | — |
| Boston Children's Hospital | Boston | Massachusetts | 02115 | — |
| Children's Mercy Hospital | Kansas City | Missouri | 64108 | — |
| Washington University in St. Louis School of Medicine | St Louis | Missouri | 63110 | — |
| Columbia University Medical Center | New York | New York | 10032 | — |
| State University of New York Upstate Medical Center | Syracuse | New York | 13210 | — |
| Nationwide Children's Hospital | Columbus | Ohio | 43205 | — |
| Doernbecher Children's Hospital | Portland | Oregon | 97239 | — |
| Vanderbilt University | Nashville | Tennessee | 37212 | — |
| Children's Medical Center of Dallas | Dallas | Texas | 75235 | — |
| University of Utah Health Sciences Center | Salt Lake City | Utah | 84132 | — |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT01736553, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted May 4, 2018 · Synced Nov 4, 2026
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Open the official record
The complete public registry record, listed eligibility criteria, and available contact information for NCT01736553 live on ClinicalTrials.gov.