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Completed Phase 3 Interventional Results available

Clinical Study of Macitentan in Patients With Pulmonary Arterial Hypertension to Psychometrically Validate the PAH-SYMPACT Instrument

ClinicalTrials.gov ID: NCT01841762

Public ClinicalTrials.gov record NCT01841762. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Sep 3, 2026, 4:18 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Multi-center, Open-label, Single-arm, Phase 3b Study of Macitentan in Patients With Pulmonary Arterial Hypertension to Psychometrically Validate the PAH-SYMPACT Instrument

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

SYMPHONY is prospective, multi-center, open-label, single-arm, Phase 3b psychometric validation study of the PAH-SYMPACT, a new quality of life questionnaire for patients with pulmonary arterial hypertension. Patients will be in the study for 5 1/2 months, 4 months of which they will receive macitentan, 10 mg, once daily. The primary objectives are to demonstrate the final content validity of the PAH SYMPACT instrument, to demonstrate the psychometric characteristics of reliability and construct validity of the PAH-SYMPACT instrument, and to demonstrate the ability of the PAH SYMPACT instrument to detect change. The secondary objective is to assess the safety of macitentan in patients with pulmonary arterial hypertension. The exploratory objective is to explore the effects of macitentan on PAH symptoms and their impact (as measured by the PAH-SYMPACT) in patients with pulmonary arterial hypertension.

Study identification

NCT ID
NCT01841762
Recruitment status
Completed
Study type
Interventional
Phase
Phase 3
Lead sponsor
Actelion
Industry
Enrollment
284 participants

Conditions and interventions

Interventions

Drug

Eligibility (public fields only)

Age range
18 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Mar 31, 2013
Primary completion
Oct 31, 2015
Completion
Oct 31, 2015
Last update posted
Feb 25, 2019

2013 – 2015

United States locations

U.S. sites
81
U.S. states
29
U.S. cities
60
Facility City State ZIP Site status
Cardiovascular Associates of the Southeast, LLC Birmingham Alabama 35243
University of Alabama at Birmingham Birmingham Alabama 35294
Pulmonary Associates, PA Phoenix Arizona 85006-2611
Mayo Clinic Arizona Phoenix Arizona 85054-4502
Cedars-Sinai Medical Center Beverly Hills California 90211
UCSF Fresno Fresno California 93701
UCSD Medical Center, Pulmonary Department La Jolla California 92093
VAGLAHS, VA Greater LA Healthcare System Los Angeles California 90073
University of California Los Angeles Los Angeles California 90095
University of California San Francisco Medical Center San Francisco California 94143
Stanford University Stanford California 94305-2200
Los Angeles Biomedical Research Institute Torrance California 90502
University of Colorado Aurora Colorado 80045
MedStar Georgetown University Hospital Washington D.C. District of Columbia 20007
Medstar Washington Hospital Center Washington D.C. District of Columbia 20010
Bay Area Cardiology Associates, P.A. Brandon Florida 33511
University of Florida Academic Health Center Gainesville Florida 32610
University of Florida College of Medicine, Jacksonville Jacksonville Florida 32209
Mayo Clinic Jacksonville Florida 32224-1865
Cleveland Clinic Florida Weston Florida 33331-3609
Georgia Regents University Augusta Georgia 30912
Georgia Clinical Research Austell Georgia 30106
Northwestern University Chicago Illinois 60611
University of Chicago Medical Chicago Illinois 60637
Advocate Health and Hospitals Corporation Oakbrook Terrace Illinois 60181
Chest Infectious Diseases and Critical Care Associates, PC Des Moines Iowa 50325-7046
University of Iowa Hospitals & Clinics Iowa City Iowa 52242
Iowa City Heart Center Iowa City Iowa 52245
University of Kansas Medical Center Kansas City Kansas 66160-0001
Veritas Clinical Specialties Topeka Kansas 66606
Kentuckiana Pulmonary Associates Louisville Kentucky 40202
University of Louisville Louisville Kentucky 40202
University of Maryland Medical Center Baltimore Maryland 21201
Johns Hopkins University Baltimore Maryland 21205
Tufts Medical Center Boston Massachusetts 02111
Boston University Medical Center Boston Massachusetts 02118
University of Michigan Ann Arbor Michigan 48109-5644
Beaumont Hospital Troy Michigan 48085
Mayo Clinic Rochester Minnesota 55905
Midwest Pulmonary Consultants Kansas City Missouri 64111
Ferrell-Duncan Clinic Springfield Missouri 65807
Washington University School of Medicine St Louis Missouri 63110
Mercy Clinic Pulmonology St Louis Missouri 63141
Clayton Sleep Institute St Louis Missouri 63143
Nebraska Pulmonary Specialties Lincoln Nebraska 68506
University of Nebraska Medical Center Omaha Nebraska 68198
Pulmonary and Critical Care Associates Union New Jersey 07083
Buffalo General Medical Center Buffalo New York 14203
Winthrop University Hospital Mineola New York 11501
North Shore-LIJ/Advance Lung Disease Clinic New Hyde Park New York 11040
Beth Israel Medical Center New York New York 10003
Columbia University Medical Center New York New York 10032
Montefiore Medical Center, Weiler Division The Bronx New York 10461
University of North Carolina at Chapel Hill Chapel Hill North Carolina 27599
Novant Health Pulmonary and Critical Care Matthews North Carolina 28105
The Christ Hospital Cincinnati Ohio 45219
UC Health/University of Cincinnati Cincinnati Ohio 45267
Cleveland Clinic Cleveland Ohio 45219
Davis Heart & Lung Research Institute Columbus Ohio 43210-1252
The Ohio State University Columbus Ohio 43221
University of Oklahoma Health Sciences Center Oklahoma City Oklahoma 73104
The Oregon Clinic Portland Oregon 97220
CDA for Oregon Pulmonary Associate Portland Oregon 97225
Oregon Health and Science University Portland Oregon 97239
Thomas Jefferson University, Division on Pulmonary and Critical Care Philadelphia Pennsylvania 19107-5109
Temple Lung Center Philadelphia Pennsylvania 19140
UPMC Pittsburgh Pennsylvania 15123
Allegheny General Hospital Pittsburgh Pennsylvania 15212-4756
Berks Schuylkill Respiratory Specialists, Ltd. Wyomissing Pennsylvania 19610
Wellspan Lung, Sleep and Critical Care York Pennsylvania 17402-8200
Sioux Falls Cardiovascular, PC Sioux Falls South Dakota 57108
Baylor Research Institute (BRI) Dallas Texas 75204
UT Southwestern Medical Center Dallas Texas 75390-8550
Baylor College of Medicine Houston Texas 77030-2348
The University of Texas Health Science Center at Houston Houston Texas 77030
Scott & White Memorial Hospital Temple Texas 76508
Inova Heart and Vascular Institue / Inova Fairfax Hospital Falls Church Virginia 22042-3307
Sentara Norfolk General Hospital Norfolk Virginia 23507
Pulmonary & Sleep Research Spokane Washington 99204
University of Wisconsin School of Medicine and Public Health Madison Wisconsin 53792
Aurora Cardiovascular Services Milwaukee Wisconsin 53215

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT01841762, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Feb 25, 2019 · Synced Sep 3, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT01841762 live on ClinicalTrials.gov.

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