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Terminated Phase 3 Interventional Results available

An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation Dystrophinopathy

ClinicalTrials.gov ID: NCT02090959

Public ClinicalTrials.gov record NCT02090959. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 17, 2026, 7:58 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 3 Extension Study of Ataluren (PTC124) in Patients With Nonsense Mutation Dystrophinopathy

Study identification

NCT ID
NCT02090959
Recruitment status
Terminated
Study type
Interventional
Phase
Phase 3
Lead sponsor
PTC Therapeutics
Industry
Enrollment
219 participants

Conditions and interventions

Eligibility (public fields only)

Age range
7 Years to 15 Years
Sex
Male
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Mar 19, 2014
Primary completion
Jun 11, 2018
Completion
Jun 11, 2018
Last update posted
Aug 10, 2020

2014 – 2018

United States locations

U.S. sites
21
U.S. states
16
U.S. cities
21
Facility City State ZIP Site status
University of California, Los Angeles Los Angeles California 90095
UC Davis Medical Center Sacramento California 95817
Stanford University Medical Center Stanford California 94305
Children's Hospital Colorado - Center for Cancer and Blood Disorders Aurora Colorado 80045
Child Neurology Center of Northwest Florida Gulf Breeze Florida 32561
Rush University Medical Center Chicago Illinois 60612
University of Iowa Iowa City Iowa 52242
University of Kansas Medical Center Kansas City Kansas 66160
Children's Hospital Boston Boston Massachusetts 02115
University of Minnesota Minneapolis Minnesota 55455
Washington University School of Medicine, Division of Endocrinology, Metabolism and Lipid Research St Louis Missouri 63110
Columbia University College of Physicians & Surgeons New York New York 10032
Children's Hospital Cincinnati Cincinnati Ohio 45229
Nationwide Children's Hospital Columbus Ohio 43209
Oregon Health & Science University Portland Oregon 97239
The Children's Hospital of Philadelphia Philadelphia Pennsylvania 19104
Children's Hospital of Pittsburgh Pittsburgh Pennsylvania 15224
Childrens Medical Center Dallas, Texas Dallas Texas 75207
Texas Children's Hospital Houston Texas 77030
University of Utah Salt Lake City Utah 84112
Seattle Children's Hospital - Childhood Cancer and Blood Disorders Seattle Washington 98105

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 37 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT02090959, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Aug 10, 2020 · Synced May 17, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT02090959 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →