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Completed Phase 1Phase 2 Interventional Results available

Safety and Efficacy of rAAV-hRS1 in Patients With X-linked Retinoschisis (XLRS)

ClinicalTrials.gov ID: NCT02416622

Public ClinicalTrials.gov record NCT02416622. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jul 21, 2026, 2:21 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Multiple-Site, Phase 1/2, Safety and Efficacy Trial of a Recombinant Adeno-associated Virus Vector Expressing Retinoschisin (rAAV2tYF-CB-hRS1) in Patients With X-linked Retinoschisis

Study identification

NCT ID
NCT02416622
Recruitment status
Completed
Study type
Interventional
Phase
Phase 1, Phase 2
Lead sponsor
Beacon Therapeutics
Industry
Enrollment
27 participants

Conditions and interventions

Interventions

  • rAAV2tYF-CB-hRS1 Biological

Biological

Eligibility (public fields only)

Age range
6 Years and older
Sex
Male
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Apr 30, 2015
Primary completion
Mar 31, 2019
Completion
May 8, 2023
Last update posted
Jun 11, 2023

2015 – 2023

United States locations

U.S. sites
9
U.S. states
8
U.S. cities
9
Facility City State ZIP Site status
University of California San Francisco, Dept. of Ophthalmology San Francisco California 94143
University of Miami - Miller School of Medicine Bascom Palmer Eye Institute Miami Florida 33136
The Wilmer Eye Institute, Johns Hopkins Hospital Baltimore Maryland 21287
Massachusetts Eye and Ear Infirmary Boston Massachusetts 02114
University of Michigan Kellogg Eye Center Ann Arbor Michigan 48105
Duke Eye Center, Duke University Medical Center Durham North Carolina 27710
Casey Eye Institute, Oregon Health and Sciences University Portland Oregon 97239
Retina Foundation of the Southwest Dallas Texas 75231
Baylor College of Medicine, Alkek Eye Center Houston Texas 77030

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT02416622, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Jun 11, 2023 · Synced Jul 21, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT02416622 live on ClinicalTrials.gov.

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