Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy
Public ClinicalTrials.gov record NCT02420379. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Official title
An Open-Label, Multi-Center Study to Evaluate the Safety, Efficacy and Tolerability of Eteplirsen in Early Stage Duchenne Muscular Dystrophy
Study identification
- NCT ID
- NCT02420379
- Recruitment status
- Completed
- Study type
- Interventional
- Phase
- Phase 2
- Lead sponsor
- Sarepta Therapeutics, Inc.
- Industry
- Enrollment
- 33 participants
Conditions and interventions
Conditions
Interventions
- eteplirsen Drug
Drug
Eligibility (public fields only)
- Age range
- 4 Years to 6 Years
- Sex
- Male
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Jun 29, 2015
- Primary completion
- Dec 16, 2018
- Completion
- Dec 16, 2018
- Last update posted
- Jan 24, 2021
2015 – 2018
United States locations
- U.S. sites
- 13
- U.S. states
- 10
- U.S. cities
- 12
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| Neuromuscular Research Center of Arizona | Phoenix | Arizona | 85028 | — |
| Ronald Reagan UCLA Medical Center | Los Angeles | California | 90095 | — |
| University of California, Davis Medical Center | Sacramento | California | 95817 | — |
| Stanford University Medical Center | Stanford | California | 94305 | — |
| University of Florida, Shands Hospital | Gainesville | Florida | 32610 | — |
| Rare Disease Research Center | Atlanta | Georgia | 30318 | — |
| Children's Hospital of Atlanta | Atlanta | Georgia | 30324 | — |
| University of Iowa Children's Hospital | Iowa City | Iowa | 52242 | — |
| St. Louis Children's Hospital | St Louis | Missouri | 63110 | — |
| Nationwide Children's Hospital | Columbus | Ohio | 43205 | — |
| Shriners Hospital for Children | Portland | Oregon | 97239 | — |
| Children's Hospital of Philadelphia | Philadelphia | Pennsylvania | 19104 | — |
| Seattle Children's Hospital | Seattle | Washington | 98105 | — |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT02420379, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted Jan 24, 2021 · Synced Jul 24, 2026
Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.
Open the official record
The complete protocol, eligibility criteria, and contact information for NCT02420379 live on ClinicalTrials.gov.