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Completed Phase 3 Interventional Results available

The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Participants Who Have Already Been Treated With ALN-TTR02 (Patisiran)

ClinicalTrials.gov ID: NCT02510261

Public ClinicalTrials.gov record NCT02510261. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jul 21, 2026, 6:04 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Multicenter, Open-Label, Extension Study to Evaluate the Long-term Safety and Efficacy of Patisiran in Patients With Familial Amyloidotic Polyneuropathy Who Have Completed a Prior Patisiran Clinical Study

Study identification

NCT ID
NCT02510261
Recruitment status
Completed
Study type
Interventional
Phase
Phase 3
Lead sponsor
Alnylam Pharmaceuticals
Industry
Enrollment
211 participants

Conditions and interventions

Conditions

Interventions

  • Patisiran Drug

Drug

Eligibility (public fields only)

Age range
18 Years to 85 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jul 15, 2015
Primary completion
Nov 22, 2022
Completion
Nov 22, 2022
Last update posted
Dec 5, 2023

2015 – 2022

United States locations

U.S. sites
14
U.S. states
11
U.S. cities
13
Facility City State ZIP Site status
Clinical Trial Site La Mesa California
Clinical Trial Site Aurora Colorado
Clinical Trial Site Jacksonville Florida 32224
Clinical Trial Site Chicago Illinois
Clinical Trial Site Baltimore Maryland
Clinical Trial Site Boston Massachusetts
Clinical Trial Site Detroit Michigan
Clinical Trial Site Rochester Minnesota
Clinical Trial Site Joplin Missouri 64804
Clinical Trial Site St Louis Missouri
Clinical Trial Site Cooperstown New York
Clinical Trial Site New York New York 10029
Clinical Trial Site New York New York 10032
Clinical Trial Site Columbus Ohio 43210

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 42 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT02510261, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Dec 5, 2023 · Synced Jul 21, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT02510261 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →