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Completed Phase 2 Interventional Results available

A Study of Recombinant AAV2/6 Human Factor 8 Gene Therapy SB-525 (PF-07055480) in Subjects With Severe Hemophilia A

ClinicalTrials.gov ID: NCT03061201

Public ClinicalTrials.gov record NCT03061201. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jul 23, 2026, 11:59 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A PHASE 1/2, OPEN-LABEL, ADAPTIVE, DOSE-RANGING STUDY TO ASSESS THE SAFETY AND TOLERABILITY OF SB-525 (PF-07055480) (RECOMBINANT AAV2/6 HUMAN FACTOR 8 GENE THERAPY) IN ADULT SUBJECTS WITH SEVERE HEMOPHILIA A

Study identification

NCT ID
NCT03061201
Recruitment status
Completed
Study type
Interventional
Phase
Phase 2
Lead sponsor
Pfizer
Industry
Enrollment
13 participants

Conditions and interventions

Conditions

Interventions

  • SB-525 (PF-07055480) Biological

Biological

Eligibility (public fields only)

Age range
18 Years and older
Sex
Male
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jun 20, 2017
Primary completion
Jul 15, 2024
Completion
Jul 15, 2024
Last update posted
Sep 29, 2025

2017 – 2024

United States locations

U.S. sites
22
U.S. states
7
U.S. cities
10
Facility City State ZIP Site status
Arkansas Children's Hospital Little Rock Arkansas 72202
City of Hope Medical Center Duarte California 91010
Midtown Ambulatory Care Center Sacramento California 95817
UC Davis Ambulatory Care Clinic Sacramento California 95817
UC Davis Comprehensive Cancer Center Sacramento California 95817
UC Davis CTSC Clinical Research Center Sacramento California 95817
UC Davis Hemophilia Treatment Center Sacramento California 95817
UC Davis Investigational Drug Services Pharmacy Sacramento California 95817
UC Davis Medical Center Sacramento California 95817
University of California, San Francisco - Investigational Drug Service (IDS) Pharmacy San Francisco California 94143-0622
University of California, San Francisco - Outpatient Hematology Clinic San Francisco California 94143
University of California, San Francisco -Moffitt Hospital San Francisco California 94143
University Of Miami Hospital and Clinics/Sylvester Comprehensive Cancer Center Miami Florida 33136
USF Health Morsani Center For Advanced Healthcare Tampa Florida 33612
Emory University School of Medicine Atlanta Georgia 30322
Hemophilia Center of Western PA Pittsburgh Pennsylvania 15213
UPMC Montefiore Clinical and Translational Research Center Pittsburgh Pennsylvania 15213
UPMC, Investigational Drug Service Pittsburgh Pennsylvania 15213
Vanderbilt University Medical Center Clinical Research Center Nashville Tennessee 37212-8646
Vanderbilt Hemostasis Treatment Clinic Nashville Tennessee 37232
Vanderbilt Hemostasis-Thrombosis Clinic Nashville Tennessee 37232
Washington Institute for Coagulation Seattle Washington 98101

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03061201, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Sep 29, 2025 · Synced Jul 23, 2026

Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.

Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03061201 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →