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Completed Phase 3 Interventional Results available

A Study to Evaluate Safety, Efficacy, and Tolerability of TEZ/IVA in Orkambi® (Lumacaftor/Ivacaftor) -Experienced Subjects With Cystic Fibrosis (CF)

ClinicalTrials.gov ID: NCT03150719

Public ClinicalTrials.gov record NCT03150719. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jun 27, 2026, 4:22 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Phase 3b, Randomized, Double-blind, Placebo-controlled, Parallel Group Study to Assess the Safety, Efficacy, and Tolerability of Tezacaftor/Ivacaftor (TEZ/IVA) in an Orkambi-experienced Population Who Are Homozygous for the F508del CFTR Mutation

Study identification

NCT ID
NCT03150719
Recruitment status
Completed
Study type
Interventional
Phase
Phase 3
Lead sponsor
Vertex Pharmaceuticals Incorporated
Industry
Enrollment
98 participants

Conditions and interventions

Interventions

  • Tezacaftor/Ivacaftor Drug
  • Ivacaftor Drug
  • Placebo Drug

Drug

Eligibility (public fields only)

Age range
12 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
May 23, 2017
Primary completion
Aug 8, 2018
Completion
Aug 8, 2018
Last update posted
Sep 11, 2019

2017 – 2018

United States locations

U.S. sites
41
U.S. states
28
U.S. cities
37
Facility City State ZIP Site status
University of Alabama at Birmingham Birmingham Alabama 35233
Phoenix Children's Hospital Phoenix Arizona 85016
UCSF - Fresno, Community Regional Medical Center Fresno California 93701
Miller Children's Hospital / Long Beach Memorial Long Beach California 90806
Children's Hospital Los Angeles Los Angeles California 90027
Rady Children's Hospital San Diego California 92123
National Jewish Health Denver Colorado 80206
Yale New Haven Hospital New Haven Connecticut 06510
Central Florida Pulmonary Group Orlando Florida 32803
Arnold Palmer Hospital Orlando Florida 32806
Tampa General Hospital Cardiac and Lung Transplant Clinic Tampa Florida 33606
Children's Speciality Services at North Druid Hills Atlanta Georgia 30324
St. Luke's CF Center of Idaho Boise Idaho 83702
Advocate Children's Hospital - Park Ridge / North Suburban Pulmonary and Critical Care Consultants Niles Illinois 60714
Southern Illinois University Springfield Illinois 62702
Riley Hospital for Children at Indiana University Health Indianapolis Indiana 46202
The University of Iowa Hospitals and Clinics Iowa City Iowa 52242
University of Kansas Medical Center Kansas City Kansas 66160
Kentucky Clinic Lexington Kentucky 40536
Tulane Medical Center New Orleans Louisiana 70112
Massachusetts General Hospital Cystic Fibrosis Center Boston Massachusetts 02114
Boston Children's Hospital Boston Massachusetts 02115
University of Mississippi Medical Center Jackson Mississippi 39216
Children's Mercy Hospital Kansas City Missouri 64108
Billings Clinic Billings Montana 59101
Mount Sinai Beth Israel New York New York 10003
New York Medical College Valhalla New York 10595
Duke University Medical Center Durham North Carolina 27710
Wake Forest University Baptist Medical Center Winston-Salem North Carolina 27157
Cleveland Clinic Foundation Cleveland Ohio 44195
University of Oklahoma Health Sciences Center Oklahoma City Oklahoma 73104
Santiago Reyes, M.D. Oklahoma City Oklahoma 73112
Drexel University College of Medicine/ Drexel Adult Cystic Fibrosis Center Philadelphia Pennsylvania 19107
Medical University of South Carolina Charleston South Carolina 29425
Vanderbilt University Medical Center Nashville Tennessee 37232
The University of Tennessee Medical Center Nashville Tennessee 37920
Dell Children's Medical Center of Central Texas Austin Texas 78723
The University of Texas Health Science Center at San Antonio San Antonio Texas 78207
University of Utah / Primary Children's Medical Center Salt Lake City Utah 84132
Children's Hospital of the King's Daughters Norfolk Virginia 23507
Children's Hospital of Richmond at VCU, Children's Pavilion Richmond Virginia 23298

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 12 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03150719, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Sep 11, 2019 · Synced Jun 27, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03150719 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →