Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy
Public ClinicalTrials.gov record NCT03179631. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Official title
A Phase 3, Randomized, Double-blind, Placebo-controlled Efficacy and Safety Study of Ataluren in Patients With Nonsense Mutation Duchenne Muscular Dystrophy and Open-Label Extension
Study identification
- NCT ID
- NCT03179631
- Recruitment status
- Completed
- Study type
- Interventional
- Phase
- Phase 3
- Lead sponsor
- PTC Therapeutics
- Industry
- Enrollment
- 360 participants
Conditions and interventions
Conditions
Interventions
- Ataluren Drug
- PLACEBO Drug
Drug
Eligibility (public fields only)
- Age range
- 5 Years and older
- Sex
- Male
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Jul 5, 2017
- Primary completion
- Mar 4, 2022
- Completion
- Jul 24, 2023
- Last update posted
- Mar 9, 2026
2017 – 2023
United States locations
- U.S. sites
- 22
- U.S. states
- 15
- U.S. cities
- 22
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| Phoenix Childrens Hospital | Phoenix | Arizona | 85016 | — |
| Children's Hospital of Los Angeles | Los Angeles | California | 90027 | — |
| University of California, San Francisco (UCSF) - Benioff Children's Hospital - Oakland | Oakland | California | 94143 | — |
| Stanford University Medical Center | Palo Alto | California | 94305 | — |
| University of California (UC) Davis Medical Center | Sacramento | California | 95817 | — |
| Loma Linda University Children's Hospital | San Bernardino | California | 92408 | — |
| Northwest Florida Clinical Research Group, LLC | Gulf Breeze | Florida | 32561 | — |
| Indiana University Health - Riley Child Neurology | Indianapolis | Indiana | 46202 | — |
| University of Kansas Medical Center | Kansas City | Kansas | 66160 | — |
| University of Michigan - CS Mott Children's Hospital | Ann Arbor | Michigan | 48109 | — |
| Children's Hospital of Michigan | Detroit | Michigan | 48201 | — |
| University of Minnesota | Minneapolis | Minnesota | 55455 | — |
| Columbia University College of Physicians & Surgeons | New York | New York | 10032 | — |
| Cincinnati Children's Hospital Medical Center | Cincinnati | Ohio | 45229 | — |
| Shriners Hospital for Children | Portland | Oregon | 97239 | — |
| University of Pittsburgh School of Medicine | Pittsburgh | Pennsylvania | 15224 | — |
| Cook Childrens Medical Center | Fort Worth | Texas | 76104 | — |
| Texas Children's Hospital | Houston | Texas | 77030 | — |
| University of Texas Health Science Center at San Antonio | San Antonio | Texas | 78229-3900 | — |
| University Of Utah | Salt Lake City | Utah | 84112 | — |
| Children's Hospital of the King's Daughters | Norfolk | Virginia | 23507 | — |
| Seattle Children's Hospital | Seattle | Washington | 98105 | — |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
Non-U.S. locations
This page focuses on the U.S. directory. The official record also lists 42 non-U.S. sites.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT03179631, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted Mar 9, 2026 · Synced May 19, 2026
Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.
Open the official record
The complete protocol, eligibility criteria, and contact information for NCT03179631 live on ClinicalTrials.gov.