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Terminated Phase 2 Interventional

A Study to Assess the Safety and Effectiveness of FLX-787 in Subjects With Charcot-Marie-Tooth Disease Experiencing Muscle Cramps.

ClinicalTrials.gov ID: NCT03254199

Public ClinicalTrials.gov record NCT03254199. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Apr 29, 2026, 9:21 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Randomized, Double-Blind, Controlled, Parallel Group Study to Evaluate the Efficacy and Safety of FLX-787-ODT for Treatment of Muscle Cramps in Adult Subjects With Charcot-Marie-Tooth Disease

Study identification

NCT ID
NCT03254199
Recruitment status
Terminated
Study type
Interventional
Phase
Phase 2
Lead sponsor
Flex Pharma, Inc.
Industry
Enrollment
27 participants

Conditions and interventions

Interventions

  • FLX-787-ODT (orally disintegrating tablet) Drug
  • Placebo ODT Drug

Drug

Eligibility (public fields only)

Age range
18 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Oct 15, 2017
Primary completion
Jul 26, 2018
Completion
Jul 26, 2018
Last update posted
Aug 28, 2018

2017 – 2018

United States locations

U.S. sites
20
U.S. states
15
U.S. cities
19
Facility City State ZIP Site status
Mayo Clinic Scottsdale Arizona 85259
University of Colorado Aurora Colorado 80045
Hospital for Special Care New Britain Connecticut 06053
University of Florida Gainesville Florida 32607
Mayo Clinic Jacksonville Florida 32224
University of South Florida Tampa Florida 33612
University of Iowa Iowa City Iowa 52242
University of Kansas Medical Center Kansas City Kansas 66160
Massachusetts General Hospital Boston Massachusetts 02114
Brighman and Women's Hospital Boston Massachusetts 02115
University of Minnesota Minneapolis Minnesota 55455
Saint Louis University St Louis Missouri 63104
Columbia University Medical Center New York New York 10032
University of Rochester Medical Center Rochester New York 14642
Oregon Health Science University Portland Oregon 97239
Penn State Milton S. Hershey Medical Center Hershey Pennsylvania 17033
Temple University Philadelphia Pennsylvania 19140
The University of Utah Salt Lake City Utah 84112
University of Vermont Medical Center Burlington Vermont 05405
Saint Luke's Rehabilitation Institute Spokane Washington 99202

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03254199, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Aug 28, 2018 · Synced Apr 29, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03254199 live on ClinicalTrials.gov.

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