A Study to Evaluate the Safety and Tolerability of PF-06939926 Gene Therapy in Duchenne Muscular Dystrophy
Public ClinicalTrials.gov record NCT03362502. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Official title
A PHASE 1B MULTICENTER, OPEN-LABEL, SINGLE ASCENDING DOSE STUDY TO EVALUATE THE SAFETY AND TOLERABILITY OF PF-06939926 IN AMBULATORY AND NON-AMBULATORY SUBJECTS WITH DUCHENNE MUSCULAR DYSTROPHY
Study identification
- NCT ID
- NCT03362502
- Recruitment status
- Terminated
- Study type
- Interventional
- Phase
- Phase 1
- Lead sponsor
- Pfizer
- Industry
- Enrollment
- 23 participants
Conditions and interventions
Conditions
Interventions
- PF-06939926 Genetic
Genetic
Eligibility (public fields only)
- Age range
- 4 Years and older
- Sex
- Male
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Jan 22, 2018
- Primary completion
- Mar 27, 2022
- Completion
- Jul 27, 2025
- Last update posted
- Sep 14, 2025
2018 – 2025
United States locations
- U.S. sites
- 22
- U.S. states
- 3
- U.S. cities
- 3
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| MRI Research Center | Los Angeles | California | 90095 | — |
| Reed Neurological Research Center | Los Angeles | California | 90095 | — |
| Ronald Reagan UCLA Medical Center (Investigational Drug Section) | Los Angeles | California | 90095 | — |
| Ronald Reagan UCLA Medical Center - Interventional Radiology | Los Angeles | California | 90095 | — |
| Ronald Reagan UCLA Medical Center Drug Information Center | Los Angeles | California | 90095 | — |
| UCLA (David Geffen School of Medicine) | Los Angeles | California | 90095 | — |
| UCLA Children's Heart Center | Los Angeles | California | 90095 | — |
| UCLA Mattel Children's Hospital | Los Angeles | California | 90095 | — |
| UCLA Medical Center | Los Angeles | California | 90095 | — |
| UCLA Outpatient Surgery Center | Los Angeles | California | 90095 | — |
| Duke Neurology | Durham | North Carolina | 27705 | — |
| Duke University Medical Center, Lenox Baker Children's Hospital | Durham | North Carolina | 27705 | — |
| Biospecimen Repository & Processing Core - BPRC | Durham | North Carolina | 27710 | — |
| Duke Cardiovascular Magnetic Resonance Center | Durham | North Carolina | 27710 | — |
| Duke Children's Hospital & Health Center | Durham | North Carolina | 27710 | — |
| Duke University Hospital Investigational Drug Services (IDS) Pharmacy | Durham | North Carolina | 27710 | — |
| CCTS Clinical Research Center | Salt Lake City | Utah | 84108 | — |
| University of Utah Imaging and Neurosciences Center | Salt Lake City | Utah | 84108 | — |
| University of Utah Hospital & Clinics Investigational Drug Services | Salt Lake City | Utah | 84112 | — |
| University of Utah Hospital | Salt Lake City | Utah | 84112 | — |
| Primary Children's Hospital | Salt Lake City | Utah | 84113 | — |
| University of Utah Clinical Neurosciences Center | Salt Lake City | Utah | 84132 | — |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT03362502, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted Sep 14, 2025 · Synced Jul 24, 2026
Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.
Open the official record
The complete protocol, eligibility criteria, and contact information for NCT03362502 live on ClinicalTrials.gov.