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No Longer Available No phase listed Expanded access

Expanded Access Program for Idebenone in Participants With Duchenne Muscular Dystrophy (DMD)

ClinicalTrials.gov ID: NCT03433807

Public ClinicalTrials.gov record NCT03433807. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Sep 6, 2026, 5:36 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Expanded Access Protocol (EAP) of Idebenone in Patients With Duchenne Muscular Dystrophy

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

The primary objective of this Expanded Access Program is to provide idebenone as a treatment for eligible participants with Duchenne Muscular Dystrophy before it is commercially available in the United States (U.S.) for the indication of DMD.

Study identification

NCT ID
NCT03433807
Recruitment status
No Longer Available
Study type
Expanded access
Phase
Not listed
Lead sponsor
Santhera Pharmaceuticals
Industry
Enrollment
Not listed

Conditions and interventions

Interventions

Drug

Eligibility (public fields only)

Age range
8 Years and older
Sex
All
Healthy volunteers
Not listed

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Not listed
Primary completion
Not listed
Completion
Not listed
Last update posted
Apr 20, 2023

United States locations

U.S. sites
12
U.S. states
12
U.S. cities
12
Facility City State ZIP Site status
Phoenix Children's Hospital Phoenix Arizona 85016
Yale New Haven Hospital New Haven Connecticut 06510
Lurie Children's Hospital of Chicago Chicago Illinois 60611
University of Iowa Iowa City Iowa 52242
University of Kansas Medical Center Kansas City Kansas 66160
Kennedy Krieger Baltimore Maryland 21287
Columbia University Pediatric Neuromuscular Center New York New York 10032
Carolina's Healthcare System Charlotte North Carolina 28207
Cincinnati Children's Hospital Medical Center Cincinnati Ohio 45229
Children's Hospital of Philadelphia Philadelphia Pennsylvania 19104
University of Virginia Children's Hospital Charlottesville Virginia 22904
St. Luke's Rehabilitation Institute Spokane Washington 99202

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03433807, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Apr 20, 2023 · Synced Sep 6, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03433807 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →