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Completed Phase 2 Interventional Results available

Dose Confirmation Trial of AAV5-hFIXco-Padua

ClinicalTrials.gov ID: NCT03489291

Public ClinicalTrials.gov record NCT03489291. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jul 22, 2026, 5:49 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Phase IIb, Open-label, Single-dose, Single-arm, Multi-center Trial to Confirm the Factor IX Activity Level of the Serotype 5 Adeno-associated Viral Vector Containing the Padua Variant of a Codon-optimized Human Factor IX Gene (AAV5-hFIXco-Padua, AMT-061) Administered to Adult Subjects With Severe or Moderately Severe Hemophilia B

Study identification

NCT ID
NCT03489291
Recruitment status
Completed
Study type
Interventional
Phase
Phase 2
Lead sponsor
CSL Behring
Industry
Enrollment
3 participants

Conditions and interventions

Conditions

Interventions

  • AAV5-hFIXco-Padua (AMT-061) Genetic

Genetic

Eligibility (public fields only)

Age range
18 Years and older
Sex
Male
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jul 23, 2018
Primary completion
Oct 29, 2018
Completion
Sep 20, 2023
Last update posted
Jun 27, 2024

2018 – 2023

United States locations

U.S. sites
4
U.S. states
3
U.S. cities
4
Facility City State ZIP Site status
Phoenix Childrens Hospital Phoenix Arizona 85016
University of California, Davis Sacramento California 95817
University of California, San Diego San Diego California 92122
University of Michigan Ann Arbor Michigan 48109

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03489291, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Jun 27, 2024 · Synced Jul 22, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03489291 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →