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Completed Phase 3 Interventional Results available

A Phase 3 Study of VX-445 Combination Therapy in Subjects With Cystic Fibrosis Heterozygous for the F508del Mutation and a Minimal Function Mutation (F/MF)

ClinicalTrials.gov ID: NCT03525444

Public ClinicalTrials.gov record NCT03525444. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Sep 2, 2026, 5:36 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 3, Randomized, Double-blind, Controlled Study Evaluating the Efficacy and Safety of VX-445 Combination Therapy in Subjects With Cystic Fibrosis Who Are Heterozygous for the F508del Mutation and a Minimal Function Mutation (F/MF)

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

This study will evaluate the efficacy of VX-445 in triple combination (TC) with tezacaftor (TEZ) and ivacaftor (IVA) in subjects with cystic fibrosis (CF) who are heterozygous for F508del and a minimal function mutation (F/MF subjects).

Study identification

NCT ID
NCT03525444
Recruitment status
Completed
Study type
Interventional
Phase
Phase 3
Enrollment
405 participants

Conditions and interventions

Interventions

Drug

Eligibility (public fields only)

Age range
12 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jun 14, 2018
Primary completion
Apr 23, 2019
Completion
Apr 23, 2019
Last update posted
May 18, 2020

2018 – 2019

United States locations

U.S. sites
53
U.S. states
29
U.S. cities
51
Facility City State ZIP Site status
Banner University of Arizona Medical Center Tucson Arizona 85724
University of Arkansas for Medical Sciences Little Rock Arkansas 72205
Miller Children's Hospital/ Long Beach Memorial Long Beach California 90806
Children's Hospital Los Angeles Los Angeles California 90027
Valley Children's Hospital/ Children's Hospital of Central California Madera California 93636
Kaiser Permanente Oakland California 94611
University of California Davis Medical Center Sacramento California 95817
UCSF Gateway Medical Center San Francisco California 94143
National Jewish Health Denver Colorado 80206
University of Florida, Shands Hospital Gainesville Florida 32610
Joe DiMaggio Cystic Fibrosis & Pulmonary Center/ Joe DiMaggio Children's Hospital/ Memorial Regional Hospital Hollywood Florida 33021
Nemours Children's Specialty Care Jacksonville Florida 32207
Central Florida Pulmonary Group Orlando Florida 32803
Nemours Children's Hospital Orlando Florida 32827
Tampa General Hospital Cardiac and Lung Transplant Clinic Tampa Florida 33606
Children's Speciality Services at North Druid Hills Atlanta Georgia 30324
Augusta University Augusta Georgia 30912
Ann & Robert Lurie Children's Hospital of Chicago Chicago Illinois 60611
Northwestern Memorial Hospital Chicago Illinois 60611
Saint Francis Medical Center/ Children's Hospital of Illinois/OSF Peoria Illinois 61637
University of Kansas Medical Center Kansas City Kansas 66160
Tulane Medical Center New Orleans Louisiana 70112
Maine Medical Partners Portland Maine 04102
Massachusetts General Hospital Cystic Fibrosis Center Boston Massachusetts 02114
Harper University Hospital Detroit Michigan 48201
Children's Respiratory and Critical Care Specialists, P.A., Children's Hospitals and Clinics of Minnesota Minneapolis Minnesota 55404
Billings Clinic Billings Montana 59101
Nebraska Medical Center Omaha Nebraska 68198
Morristown Medical Center Morristown New Jersey 07960
University of New Mexico Clinical & Translational Science Center Albuquerque New Mexico 87131
Mount Sinai Beth Israel New York New York 10003
New York Medical College Valhalla New York 10595
UNC Marsico Clinical Research Center Chapel Hill North Carolina 27517
Akron Children's Hospital Akron Ohio 44308
UC Health Holmes Cincinnati Ohio 45220
University Hospitals Cleveland Medical Center/ Rainbow Babies and Children's Hospital Cleveland Ohio 44106
Nationwide Children's Hospital Columbus Ohio 43205
Dayton Children's Hospital Dayton Ohio 45404
ProMedica Toledo Hospital/ Toledo Children's Hospital/ Pediatric Pulmonary & Cystic Fibrosis Center Toledo Ohio 43606
University of Oklahoma Health Sciences Center Oklahoma City Oklahoma 73104
Children's Hospital of Philadelphia Philadelphia Pennsylvania 19104
Medical University of South Carolina Charleston South Carolina 29425
Austin Children's Chest Associates Austin Texas 78723
The University of Texas Southwestern Medical Center Dallas Texas 75390
The University of Texas Health Science Center at Tyler Tyler Texas 75708
Vermont Lung Center Colchester Vermont 05446
University of Virginia Primary Care Center Charlottesville Virginia 22908
Children's Hospital of the King's Daughters Norfolk Virginia 23507
Children's Hospital of Richmond at VCU, Children's Pavilion Richmond Virginia 23298
University of Washington Medical Center Seattle Washington 98195
West Virginia University Morgantown West Virginia 26506
University of Wisconsin Hospitals and Clinics Madison Wisconsin 53792
CTSI Adult Translational Research Unit/Medical College of Wisconsin/Froedtert Hospital Milwaukee Wisconsin 53226

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 62 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03525444, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted May 18, 2020 · Synced Sep 2, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03525444 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →