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Terminated Phase 3 Interventional Results available

An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy

ClinicalTrials.gov ID: NCT03532542

Public ClinicalTrials.gov record NCT03532542. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 11, 2026, 4:32 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Long-term, Open-label Extension Study for Patients With Duchenne Muscular Dystrophy Enrolled in Clinical Trials Evaluating Casimersen or Golodirsen

Study identification

NCT ID
NCT03532542
Recruitment status
Terminated
Study type
Interventional
Phase
Phase 3
Lead sponsor
Sarepta Therapeutics, Inc.
Industry
Enrollment
171 participants

Conditions and interventions

Interventions

  • Casimersen Drug
  • Golodirsen Drug

Drug

Eligibility (public fields only)

Age range
7 Years to 23 Years
Sex
Male
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Aug 1, 2018
Primary completion
Jul 25, 2023
Completion
Jul 25, 2023
Last update posted
Sep 18, 2024

2018 – 2023

United States locations

U.S. sites
25
U.S. states
19
U.S. cities
24
Facility City State ZIP Site status
Neuromuscular Research Center Phoenix Arizona 85028
Children's Hospital Los Angeles Los Angeles California 90027
University of California Los Angeles Los Angeles California 90095
Stanford Neuroscience Health Center Palo Alto California 94304
Rady Children's Hospital- San Diego San Diego California 92123
UF Health: University of Florida Clinical Research Center Gainesville Florida 32610
NW Florida Clinical Research Group, LLC Gulf Breeze Florida 32561
Rare Disease Research, LLC Atlanta Georgia 30318
Ann and Robert H Lurie Childrens Hospital of Chicago Chicago Illinois 60611
University of Iowa Childrens Hospital Iowa City Iowa 52242
University of Kansas Medical Center Kansas City Kansas 66160
Kennedy Krieger Institute Baltimore Maryland 21205
Boston Children's Hospital Boston Massachusetts 02115
St. Louis Children's Hospital St Louis Missouri 63110
Las Vegas Clinic Las Vegas Nevada 89145
University of Rochester Medical Center - Department of Neurology Rochester New York 14642
Cincinnati Children's Hospital Medical Center Cincinnati Ohio 45229
Abigail Wexner Research Institute at Nationwide Children's Hospital Columbus Ohio 43205
Shriners Hospital for Children Portland Oregon 97239
Children's Hospital of Pittsburgh of UPMC Pittsburgh Pennsylvania 15224
Children's Medical Center Dallas Dallas Texas 75207
Texas Children's Hospital Houston Texas 77030
University of Utah - PPDS Salt Lake City Utah 84132
Children's Hospital of The King's Daughters Norfolk Virginia 23510
Children's Hospital of Wisconsin, Corporate Center Suite 540 Milwaukee Wisconsin 53226

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 25 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03532542, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Sep 18, 2024 · Synced May 11, 2026

Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.

Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03532542 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →