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Completed Phase 2 Interventional

Study Assessing PTI-428 Safety, Tolerability, Pharmacokinetics and Effect in Subjects With Cystic Fibrosis

ClinicalTrials.gov ID: NCT03591094

Public ClinicalTrials.gov record NCT03591094. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jun 26, 2026, 1:30 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 2, Multicenter, Randomized, Double-Blind, Placebo-Controlled Study to Assess the Safety, Tolerability, Pharmacokinetics, and Effect of PTI-428 in Subjects With Cystic Fibrosis

Study identification

NCT ID
NCT03591094
Recruitment status
Completed
Study type
Interventional
Phase
Phase 2
Lead sponsor
Proteostasis Therapeutics, Inc.
Industry
Enrollment
40 participants

Conditions and interventions

Interventions

  • PTI-428 Drug
  • Placebo Drug

Drug

Eligibility (public fields only)

Age range
18 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Aug 20, 2018
Primary completion
Feb 17, 2019
Completion
Feb 17, 2019
Last update posted
Feb 26, 2020

2018 – 2019

United States locations

U.S. sites
26
U.S. states
21
U.S. cities
24
Facility City State ZIP Site status
University of Alabama at Birmingham Birmingham Alabama 35233
University of Arizona Tucson Arizona 85724
Stanford University Stanford California 94305
National Jewish Health Denver Colorado 80206
Central Florida Pulmonary Group Altamonte Springs Florida 32701
Northwestern University Chicago Illinois 60611
Cystic Fibrosis Center, Children's Hospital of Illinois at OSF Saint Francis Medical Center Peoria Illinois 61637
University of Iowa, Roy J and Lucille A Carver College of Medicine Iowa City Iowa 52242
Universitey of Louisville, Kosair Charities Pediatric Clinical Research Unit Louisville Kentucky 40202
Maine Medical Center Portland Maine 04102
Massachusetts General Hospital Boston Massachusetts 02114
Boston Children's Hospital Boston Massachusetts 02115
Michigan Medicine, University of Michigan Ann Arbor Michigan 48109
University of Minnesota Minneapolis Minnesota 55455
Children's Mercy Hospital Kansas City Missouri 64108
Dartmouth Hitchcock Medical Center Manchester New Hampshire 03104
Mount Sinai Beth Israel New York New York 10003
Columbia University Medical Center New York New York 10032
New York Medical College Valhalla New York 10595
Duke University Medical Center Durham North Carolina 27710
Akron Children's Hospital Akron Ohio 44308
Nationwide Children's Hospital Columbus Ohio 43205
Children's Hospital of Pittsburgh of UPMC Pittsburgh Pennsylvania 15224
Medical University of South Carolina Charleston South Carolina 29425
The University of Texas Health Science Center at Tyler - Center for Clinical Research Tyler Texas 75708
University of Utah Salt Lake City Utah 84132

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03591094, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Feb 26, 2020 · Synced Jun 26, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03591094 live on ClinicalTrials.gov.

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