Independent directory Public ClinicalTrials.gov records United States
ClinicalTrials.gov record
Completed No phase listed Observational

Clinical Outcome of Triheptanoin Treatment in Patients With Long-chain Fatty Acid Oxidation Disorders (LC-FAOD) Treated Under Expanded Access Program

ClinicalTrials.gov ID: NCT03768817

Public ClinicalTrials.gov record NCT03768817. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Sep 6, 2026, 4:19 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Retrospective Chart Review Study to Assess the Clinical Outcome of Triheptanoin Treatment in Patients With Long-chain Fatty Acid Oxidation Disorders (LC-FAOD) Treated Under Expanded Access Program

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

The primary objective of the study is to evaluate the clinical outcomes for the trigger event of patients who receive triheptanoin in the emergency Investigational New Drug (eIND) program.

Study identification

NCT ID
NCT03768817
Recruitment status
Completed
Study type
Observational
Phase
Not listed
Lead sponsor
Ultragenyx Pharmaceutical Inc
Industry
Enrollment
20 participants

Conditions and interventions

Eligibility (public fields only)

Age range
Not listed
Sex
All
Healthy volunteers
Not listed

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jan 29, 2019
Primary completion
Jun 7, 2020
Completion
Jun 7, 2020
Last update posted
Aug 27, 2020

2019 – 2020

United States locations

U.S. sites
15
U.S. states
11
U.S. cities
14
Facility City State ZIP Site status
Children's Hospital of Los Angeles Los Angeles California 90027
Kaiser Permanente Los Angeles California 90027
Children's Hospital of Orange County Orange California 92868
Stanford University Palo Alto California 94304
Yale University New Haven Connecticut 06511
Children's National Hospital Washington D.C. District of Columbia 20010
University of South Florida Tampa Florida 33606
Emory University Atlanta Georgia 30322
Boston Children's Hospital Boston Massachusetts 02115
University of Minnesota Masonic Children's Hospital Minneapolis Minnesota 55455
Duke University Durham North Carolina 27710
Oregon Health and Science University Portland Oregon 97239
Children's Hospital of Philadelphia Philadelphia Pennsylvania 19104
UPMC Children's Hospital of Pittsburgh Pittsburgh Pennsylvania 15224
Seattle Children's Hospital Seattle Washington 98105

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT03768817, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Aug 27, 2020 · Synced Sep 6, 2026

Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.

Open the official record

The complete protocol, eligibility criteria, and contact information for NCT03768817 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →