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Completed Phase 3 Interventional Results available

A Phase 3 Study of VX-445 Combination Therapy in Cystic Fibrosis (CF) Subjects Heterozygous for F508del and a Gating or Residual Function Mutation (F/G and F/RF Genotypes)

ClinicalTrials.gov ID: NCT04058353

Public ClinicalTrials.gov record NCT04058353. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jun 26, 2026, 5:58 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 3, Randomized, Double-blind, Controlled Study Evaluating the Efficacy and Safety of VX-445 Combination Therapy in Subjects With Cystic Fibrosis Who Are Heterozygous for the F508del Mutation and a Gating or Residual Function Mutation (F/G and F/RF Genotypes)

Study identification

NCT ID
NCT04058353
Recruitment status
Completed
Study type
Interventional
Phase
Phase 3
Lead sponsor
Vertex Pharmaceuticals Incorporated
Industry
Enrollment
271 participants

Conditions and interventions

Interventions

  • ELX/TEZ/IVA Drug
  • IVA Drug
  • TEZ/IVA Drug

Drug

Eligibility (public fields only)

Age range
12 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Aug 27, 2019
Primary completion
Jun 11, 2020
Completion
Jun 11, 2020
Last update posted
Jul 1, 2021

2019 – 2020

United States locations

U.S. sites
37
U.S. states
24
U.S. cities
35
Facility City State ZIP Site status
University of Alabama at Birmingham Birmingham Alabama 35233
Banner University of Arizona Medical Center Tucson Arizona 85724
Miller Children's Hospital / Long Beach Memorial Long Beach California 90806
Stanford University Palo Alto California 94304
University of California Davis Medical Center Sacramento California 95817
University of California San Francisco, Lung Transplant Program San Francisco California 94143
National Jewish Health Denver Colorado 80206
University of Miami Miller School of Medicine Miami Florida 33136
Central Florida Pulmonary Group, PA Orlando Florida 32803
Indiana University Indianapolis Indiana 46202
The University of Iowa Hospitals and Clinics Iowa City Iowa 52242
University of Kansas Medical Center Kansas City Kansas 66160
University of Kentucky Lexington Kentucky 40536
Massachusetts General Hospital Cystic Fibrosis Center Clinical Rsearch Center Boston Massachusetts 02114
Boston Children's Hospital Boston Massachusetts 02115
Michigan Medicine Ann Arbor Michigan 48109-5212
University of Minnesota Minneapolis Minnesota 55455
Washington University School of Medicine / St. Louis Children's Hospital St Louis Missouri 63110
Dartmouth Hitchcock Medical Center Lebanon New Hampshire 03756
Northwell Health- Long Island Jewish Medical Center New Hyde Park New York 11040
Mount Sinai Beth Israel New York New York 10003
Columbia University Medical Center New York New York 10032
University of North Carolina Hospitals Chapel Hill North Carolina 27514
UC Health Holmes Cincinnati Ohio 45220
Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center Cleveland Ohio 44106
Nationwide Children's Hospital Columbus Ohio 43205
ProMedica Toledo Hospital/Toledo Children's Hospital/Pediatric Pulmonary & Cystic Fibrosis Center Toledo Ohio 43606
University of Oklahoma Health Sciences Center Oklahoma City Oklahoma 73104
Oregon Health & Science University Portland Oregon 97239
Children's Hospital of Philadelphia Philadelphia Pennsylvania 19104
Children's Hospital of Pittsburgh of UPMC Pittsburgh Pennsylvania 15224
Dell Children's Medical Group Austin Texas 78723
The University of Texas Southwestern Medical Center Dallas Texas 75390
Texas Children's Hospital Houston Texas 77030
University of Utah / Primary Children's Medical Center Salt Lake City Utah 84132
University of Washington Medical Center Seattle Washington 98195
University of Wisconsin Hospital and Clinics Madison Wisconsin 53792

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 56 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT04058353, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Jul 1, 2021 · Synced Jun 26, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT04058353 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →