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Completed No phase listed Observational

A Multicenter Observational Study to Evaluate the Effectiveness of Patisiran in Patients With Polyneuropathy of ATTRv Amyloidosis With a V122I or T60A Mutation

ClinicalTrials.gov ID: NCT04201418

Public ClinicalTrials.gov record NCT04201418. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Oct 21, 2026, 9:47 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 4 Multicenter Observational Study to Evaluate the Effectiveness of Patisiran in Patients With Polyneuropathy of Hereditary Transthyretin-Mediated (ATTRv) Amyloidosis With a V122I or T60A Mutation

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

To evaluate the effectiveness of patisiran in patients with ATTRv amyloidosis with polyneuropathy who have a V122I or T60A mutation.

Study identification

NCT ID
NCT04201418
Recruitment status
Completed
Study type
Observational
Phase
Not listed
Lead sponsor
Alnylam Pharmaceuticals
Industry
Enrollment
67 participants

Conditions and interventions

Eligibility (public fields only)

Age range
18 Years and older
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Dec 18, 2019 (Actual)
Primary completion
May 24, 2022 (Actual)
Completion
May 24, 2022 (Actual)
Last update posted
Jun 6, 2022

2019 – 2022

United States locations

U.S. sites
27
U.S. states
17
U.S. cities
25
Facility City State ZIP Site status
Clinical Trial Site Los Angeles California 90095 —
Clinical Trial Site San Diego California 92103 —
Clinical Trial Site Aurora Colorado 80045 —
Clinical Trial Site Farmington Connecticut 06030 —
Clinical Trial Site Jacksonville Florida 32224 —
Clinical Trial Site Tampa Florida 33609 —
Clinical Trial Site Braselton Georgia 30517 —
Clinical Trial Site Macon Georgia 31201 —
Clinical Trial Site Chicago Illinois 60611 —
Clinical Trial Site Chicago Illinois 60612 —
Clinical Trial Site Boston Massachusetts 02111 —
Clinical Trial Site Detroit Michigan 48202 —
Clinical Trial Site Jackson Mississippi 39216 —
Clinical Trial Site Kansas City Missouri 64111 —
Clinical Trial Site Omaha Nebraska 68198 —
Clinical Trial Site Chapel Hill North Carolina 27599 —
Clinical Trial Site Charlotte North Carolina 28207 —
Clinical Trial Site Columbus Ohio 43210 —
Clinical Trial Site Allentown Pennsylvania 18103 —
Clinical Trial Site Bethlehem Pennsylvania 18015 —
Clinical Trial Site Lancaster Pennsylvania 17602 —
Clinical Trial Site Pittsburgh Pennsylvania 15212 —
Clinical Trial Site Pittsburgh Pennsylvania 15232 —
Clinical Trial Site Germantown Tennessee 38138 —
Clinical Trial Site Austin Texas 78756 —
Clinical Trial Site San Antonio Texas 78229 —
Clinical Trial Site Milwaukee Wisconsin 53226 —

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT04201418, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Jun 6, 2022 · Synced Oct 21, 2026

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Open the official record

The complete public registry record, listed eligibility criteria, and available contact information for NCT04201418 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →