Expanded Access Protocol for Adults and Pediatric Patients With Sickle Cell Disease Who Have No Alternative Treatment Options
Public ClinicalTrials.gov record NCT04724421. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Brief summary
Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.
The objective of this Expanded Access Protocol (EAP) is to provide voxelotor for the treatment of sickle cell disease (SCD): The study GBT440-041 is the EAP for pediatric patients aged 6 months to 11 years who have no alternative treatment options and are ineligible to participate in a clinical trial of voxelotor and the study C5341057 is the EAP for adults/adolescents 12 years of age and older for patients who cannot satisfactorily be treated with an authorized medicinal product
Study identification
- NCT ID
- NCT04724421
- Recruitment status
- No Longer Available
- Study type
- Expanded access
- Phase
- Not listed
- Enrollment
- Not listed
Conditions and interventions
Conditions
Eligibility (public fields only)
- Age range
- 6 Months to 11 Years
- Sex
- All
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Not listed
- Primary completion
- Not listed
- Completion
- Not listed
- Last update posted
- Nov 20, 2024
United States locations
- U.S. sites
- 33
- U.S. states
- 16
- U.S. cities
- 23
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| Phoenix Children's Hospital | Phoenix | Arizona | 85016 | — |
| Rady Children's Hospital San Diego | San Diego | California | 92123 | — |
| Nemours/Alfred I. duPont Hospital for Children | Wilmington | Delaware | 19803 | — |
| Children's National Hospital / Children's National Health System | Washington D.C. | District of Columbia | 20010 | — |
| Children's National Medical Center | Washington D.C. | District of Columbia | 20010 | — |
| Baptist Medical Center/Wolfson Children's Hospital | Jacksonville | Florida | 32207 | — |
| Nemours Children's Health, Jacksonville | Jacksonville | Florida | 32207 | — |
| Nemours Children's Hospital | Orlando | Florida | 32827 | — |
| Children's Healthcare of Atlanta Scottish Rite | Atlanta | Georgia | 30342 | — |
| AU Medical Center Clinical Research Pharmacy | Augusta | Georgia | 30912 | — |
| Augusta University | Augusta | Georgia | 30912 | — |
| Children's Hospital of Georgia | Augusta | Georgia | 30912 | — |
| Memorial Health University Medical Center | Savannah | Georgia | 31404 | — |
| Tulane Lakeside | Metairie | Louisiana | 70001 | — |
| Tulane University Hospitals and Clinics | New Orleans | Louisiana | 70112 | — |
| Children's Hospital | New Orleans | Louisiana | 70118 | — |
| Childrens Hospital of NOLA | New Orleans | Louisiana | 70118 | — |
| University Of Michigan Hospitals | Ann Arbor | Michigan | 48109 | — |
| Rutgers Cancer Institute of New Jersey | New Brunswick | New Jersey | 08901 | — |
| Newark Beth Israel Medical Center & Children's Hospital of New Jersey | Newark | New Jersey | 07112 | — |
| BronxCare Health System | The Bronx | New York | 10457 | — |
| Jacobi Medical Center | The Bronx | New York | 10461 | — |
| East Carolina University Brody School of Medicine(ECU) | Greenville | North Carolina | 27834 | — |
| ECU Physicians, Brody Outpatient Clinic | Greenville | North Carolina | 27834 | — |
| University Hospitals Cleveland Medical Center | Cleveland | Ohio | 44106 | — |
| Medical University of South Carolina: Investigational Drug Services Pharmacy | Charleston | South Carolina | 29425 | — |
| Medical University of South Carolina: Shawn Jenkins Women's and Children's Hospital | Charleston | South Carolina | 29425 | — |
| Medical University of South Carolina | Charleston | South Carolina | 29425 | — |
| Prisma Health - Upstate | Greenville | South Carolina | 29605 | — |
| St. Jude Children's Research Hospital | Memphis | Tennessee | 38105 | — |
| Cook Children's Health Care System | Fort Worth | Texas | 76104 | — |
| Pediatric Specialists of Virginia (Inova Ashburn HealthPlex) | Ashburn | Virginia | 20148 | — |
| Pediatric Specialists of Virginia (Schar Cancer Institute) | Fairfax | Virginia | 22031 | — |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
Non-U.S. locations
This page focuses on the U.S. directory. The official record also lists 4 non-U.S. sites.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT04724421, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted Nov 20, 2024 · Synced Oct 17, 2026
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Open the official record
The complete public registry record, listed eligibility criteria, and available contact information for NCT04724421 live on ClinicalTrials.gov.