A Research Study on How Well Concizumab Works for You if You Have Haemophilia A or B With or Without Inhibitors
Public ClinicalTrials.gov record NCT05135559. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.
Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.
Official title
Open-label Study Investigating Efficacy, Safety and Pharmacokinetics of Concizumab Prophylaxis in Children Below 12 Years With Haemophilia A or B With or Without Inhibitors
Brief summary
Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.
This study will test how well a new medicine called concizumab works for participants who have haemophilia A or B with or without inhibitors. The purpose is to show that concizumab can prevent bleeds and is safe to use. Participants will have to inject the study medicine every day under the skin with a pen-injector. The study will last for at least 2 years and up to about 4 years. The length of time the participant will be in the study depends on if the study medicine will be available for purchase in their country.
Study identification
- NCT ID
- NCT05135559
- Recruitment status
- Active, not recruiting
- Study type
- Interventional
- Phase
- Phase 3
- Enrollment
- 153 participants
Conditions and interventions
Eligibility (public fields only)
- Age range
- Not listed
- Sex
- All
- Healthy volunteers
- Healthy volunteers not accepted
This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.
Study timeline
- Start date
- Mar 24, 2022 (Actual)
- Primary completion
- Apr 21, 2026 (Actual)
- Completion
- Nov 2, 2029 (Estimated)
- Last update posted
- Sep 18, 2026
2022 – 2029
United States locations
- U.S. sites
- 19
- U.S. states
- 15
- U.S. cities
- 17
| Facility | City | State | ZIP | Site status |
|---|---|---|---|---|
| Rady Childrens Hosp San Diego | San Diego | California | 92123 | — |
| University of Colorado Hospital | Aurora | Colorado | 80045 | — |
| Arnold Palmer Children's Hospital | Orlando | Florida | 32806 | — |
| Nemours Child Orlando Hem/Onc. | Orlando | Florida | 32827 | — |
| Augusta Univ/Childrens Hosp-GA | Augusta | Georgia | 30912 | — |
| Memorial Health University Medical Center | Savannah | Georgia | 31404 | — |
| Childrens Hospital of Chicago | Chicago | Illinois | 60611 | — |
| Indiana Hemophilia-Thromb Ctr | Indianapolis | Indiana | 46260 | — |
| Children's Hosp-New Orleans | New Orleans | Louisiana | 70118 | — |
| Ochsner Clinic Foundation | New Orleans | Louisiana | 70121 | — |
| The Children's Mercy Hospital | Kansas City | Missouri | 64108 | — |
| Children's Nebraska | Omaha | Nebraska | 68114 | — |
| ECU Sickle Cell Comp Clinic | Greenville | North Carolina | 27834 | — |
| Nationwide Children's Hospital | Columbus | Ohio | 43205 | — |
| St Christopher Hosp for Child | Philadelphia | Pennsylvania | 19134 | — |
| Monroe Carell Jr. Children's Hospital at Vanderbilt | Nashville | Tennessee | 37232 | — |
| Cook Children's Hospital-Hematology-Oncology | Fort Worth | Texas | 76104 | — |
| Texas Children's Hospital_Houston | Houston | Texas | 77030 | — |
| Pediatrics Hematology/Oncology Clinic Battle Building | Charlottesville | Virginia | 22908 | — |
Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.
Non-U.S. locations
This page focuses on the U.S. directory. The official record also lists 72 non-U.S. sites.
About this trial record page
- What this page shows
- Public field values for ClinicalTrials.gov record NCT05135559, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
- What this page does not do
- No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
- Where the data comes from
- Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
- Last refresh
- Last update posted Sep 18, 2026 · Synced Oct 21, 2026
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Open the official record
The complete public registry record, listed eligibility criteria, and available contact information for NCT05135559 live on ClinicalTrials.gov.